Not applicableStudy completedNCT00351156What this trial is testingStudy to Evaluate Blood Cell Lines From Patients With Gaucher DiseaseWho this might be right forGaucher Disease Amicus Therapeutics 50
Testing effectiveness (Phase 2)Study completedNCT00679289What this trial is testingPhase II Study of KW2871 Combined With High Dose Interferon-α2b in Patients With Metastatic MelanomaWho this might be right forMetastatic MelanomaCutaneous Melanoma Ludwig Institute for Cancer Research 36
Early research (Phase 1)Study completedNCT03159117What this trial is testingPfizer PF-06688992 in Patients With Stage III or Stage IV MelanomaWho this might be right forMelanoma Memorial Sloan Kettering Cancer Center 7
Large-scale testing (Phase 3)WithdrawnNCT05815004What this trial is testingAn Efficacy and Safety Study of AVR-RD-02 Compared to Enzyme Replacement Therapy for Treatment of Gaucher Disease Type 3Who this might be right forGaucher Disease, Type 3 AVROBIO
Testing effectiveness (Phase 2)Not Yet RecruitingNCT07715084What this trial is testingStudy to Evaluate the Efficacy and Safety of Nizubaglustat (AZ-3102) in Patients With Gaucher Disease Type 3 (GD3)Who this might be right forGaucher Disease Type 3 Azafaros B.V. 20
Not applicableLooking for participantsNCT03240653What this trial is testingGaucherite - A Study to Stratify Gaucher DiseaseWho this might be right forGaucher Disease, Type IGaucher Disease, Type III Cambridge University Hospitals NHS Foundation Trust 250
Not applicableEnrolling By InvitationNCT05368038What this trial is testingScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening ProgramWho this might be right forAcid Sphingomyelinase DeficiencyCeroid Lipofuscinosis, Neuronal, 2Cerebrotendinous Xanthomatosis+11 more Albert Einstein College of Medicine 100,000
Not applicableStudy completedNCT03519646What this trial is testingEliglustat on Gaucher Disease Type IIIBWho this might be right forGaucher Disease, Type III National Taiwan University Hospital 4
Large-scale testing (Phase 3)Study completedNCT03485677What this trial is testingSafety and Efficacy of Eliglustat With or Without Imiglucerase in Pediatric Patients With Gaucher Disease (GD) Type 1 and Type 3Who this might be right forGaucher's Disease Type IGaucher's Disease Type III Sanofi 57
Not applicableAvailableNCT07675031What this trial is testingManaged Access Program of Venglustat in Pediatric and Adult Patients With Type 3 Gaucher Disease (GD3).Who this might be right forType 3 Gaucher Disease Sanofi
Not applicableLooking for participantsNCT05619900What this trial is testingRegistry of Patients Diagnosed With Lysosomal Storage DiseasesWho this might be right forMucopolysaccharidosis IMucopolysaccharidosis IIMucopolysaccharidosis IV A+5 more University of California, San Francisco 250
Testing effectiveness (Phase 2)Study completedNCT01141491What this trial is testingTrivalent Ganglioside Vaccine With Immunological Adjuvant or Immunological Adjuvant Alone in Metastatic Sarcoma Patients Who Are Rendered Disease FreeWho this might be right forSarcoma MabVax Therapeutics, Inc. 136
Testing effectiveness (Phase 2)Study completedNCT00911560What this trial is testingBivalent Vaccine With Escalating Doses of the Immunological Adjuvant OPT-821, in Combination With Oral β-glucan for High-Risk NeuroblastomaWho this might be right forNeuroblastoma Memorial Sloan Kettering Cancer Center 374
Not applicableLooking for participantsNCT05586243What this trial is testingMAGNETIC RESONANCE SPECTROSCOPY BIOMARKERS IN TYPE 3 GAUCHER DISEASE (GD3)Who this might be right forGaucher Disease, Type 3 University of Minnesota 5
Not applicableStudy completedNCT00001289What this trial is testingEffects of Enzyme Replacement in Gaucher's DiseaseWho this might be right forGaucher's Disease National Institute of Neurological Disorders and Stroke (NINDS) 70
Testing effectiveness (Phase 2)Ended earlyNCT03746587What this trial is testingStudy of Arimoclomol in Patients Diagnosed With Gaucher Disease Type 1 or 3Who this might be right forGaucher Disease, Type 1Gaucher Disease, Type 3 ZevraDenmark 39
Testing effectiveness (Phase 2)UnknownNCT05447494What this trial is testingPhase 1/2 Study of CAN103 in Subjects With Gaucher DiseaseWho this might be right forGaucher Disease, Type 1Gaucher Disease, Type 3 CANbridge (Suzhou) Bio-pharma Co., Ltd. 40
Not applicableEnrolling By InvitationNCT06627543What this trial is testingEffect of Enzyme Replacement Therapy on Cardiac Function in Children With Gaucher Disease Type 3Who this might be right forGaucher Disease Type 3 Noha Osman 44
Testing effectiveness (Phase 2)Active Not RecruitingNCT02843035What this trial is testingVenglustat in Combination With Cerezyme in Adult Patients With Gaucher Disease Type 3 With Venglustat Monotherapy ExtensionWho this might be right forGaucher Disease Type 1Gaucher Disease Type 3 Genzyme, a Sanofi Company 12
Large-scale testing (Phase 3)WithdrawnNCT01161914What this trial is testingThe Safety and Efficacy Study of ISU302 in Patient With Type I Gaucher DiseaseWho this might be right forGaucher Disease ISU Abxis Co., Ltd.