Not applicableLooking for participantsNCT03190837What this trial is testingA Long-term Follow-up Study of Gaucher DiseaseWho this might be right forGaucher Disease Duke University 200
Early research (Phase 1)Ended earlyNCT00875160What this trial is testingA Study in Type 1 Gaucher Patients to Evaluate the Pharmacokinetics, Safety and Pharmacodynamics of AT2101Who this might be right forType 1 Gaucher Disease Amicus Therapeutics 1
Not applicableUnknownNCT02120235What this trial is testingInvestigating Lysosomal Storage Diseases in Minority GroupsWho this might be right forLysosomal Storage DisordersGaucher DiseaseFabry Disease+2 more O & O Alpan LLC 20,000
Testing effectiveness (Phase 2)UnknownNCT05447494What this trial is testingPhase 1/2 Study of CAN103 in Subjects With Gaucher DiseaseWho this might be right forGaucher Disease, Type 1Gaucher Disease, Type 3 CANbridge (Suzhou) Bio-pharma Co., Ltd. 40
Not applicableStudy completedNCT04050137What this trial is testingTherapeutic Exercise to Treat Neuropathic PainWho this might be right forGaucher DiseaseFabry Disease Universidad de Zaragoza 5
Testing effectiveness (Phase 2)Looking for participantsNCT06818838What this trial is testingA Clinical Study Evaluating LY-M001 Injection in the Treatment of Adult Patients With Type I Gaucher DiseaseWho this might be right forGaucher Disease Type 1 Lingyi Biotech Co., Ltd. 12
Not applicableUnknownNCT00005900What this trial is testingStudy of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell TransplantationWho this might be right forI Cell DiseaseFucosidosisGloboid Cell Leukodystrophy+9 more Fairview University Medical Center 10
Not applicableLooking for participantsNCT03333200What this trial is testingLongitudinal Study of Neurodegenerative DisordersWho this might be right forMLDKrabbe DiseaseALD+24 more University of Pittsburgh 1,500
Large-scale testing (Phase 3)Study completedNCT02770625What this trial is testingPhase III Study of ISU302 in Patients With Type 1 Gaucher DiseaseWho this might be right forGaucher Disease, Type 1 ISU Abxis Co., Ltd. 8
Not applicableStudy completedNCT02650219What this trial is testingAuto-antibodies Prevalence and CD1 Role in Gaucher DiseaseWho this might be right forGaucher Disease Hospital St. Joseph, Marseille, France 60
Testing effectiveness (Phase 2)Active Not RecruitingNCT06545136What this trial is testingLong Term Follow-up Study of Type-1 Gaucher Subjects Post FLT201 Dose (GALILEO-2)Who this might be right forGaucher Disease, Type 1 Spur Therapeutics 75
Early research (Phase 1)Study completedNCT02536937What this trial is testingThe Effects of Renal Impairment on the Pharmacokinetics and Tolerability of Eliglustat TartrateWho this might be right forGaucher Disease Sanofi 32
Not applicableStudy completedNCT04997772What this trial is testingDigital Health Platform Customized for Patients With Gaucher DiseaseWho this might be right forGaucher DiseasePatient Reported Outcome Shoshana Vilk 80
Not applicableStudy completedNCT01358474What this trial is testingDetecting Dopaminergic Deficits in Individuals At-risk for ParkinsonismWho this might be right forParkinson DiseaseGaucher DiseaseIdiopathic Rapid Eye Movement Sleep Disorder University of Minnesota 56
Not applicableApproved For MarketingNCT00954460What this trial is testingTreatment Protocol of Velaglucerase Alfa for Patients With Type 1 Gaucher DiseaseWho this might be right forGaucher Disease, Type 1 Shire
Not applicableLooking for participantsNCT03291223What this trial is testingGaucher Disease Outcome Survey (GOS)Who this might be right forGaucher Disease Shire 1,257
Post-approval studies (Phase 4)Study completedNCT02574286What this trial is testingStudy of the Effect of Velaglucerase Alfa (VPRIV®) on Bone-related Pathology in Treatment-naïve Participants With Type 1 Gaucher DiseaseWho this might be right forGaucher Disease Shire 21
Testing effectiveness (Phase 2)Study completedNCT00391625What this trial is testingOpen-Label Extension Study Evaluating Long Term Safety in Patients With Type 1 Gaucher Disease Receiving DRX008A (ERT)Who this might be right forGaucher Disease Shire 10
Large-scale testing (Phase 3)Study completedNCT01422187What this trial is testingExtension Study of Taliglucerase Alfa in Adult Subjects With Gaucher DiseaseWho this might be right forGaucher Disease Pfizer 19
Testing effectiveness (Phase 2)Study completedNCT01685216What this trial is testingEfficacy and Safety Study of Velaglucerase Alfa in Children and Adolescents With Type 3 Gaucher DiseaseWho this might be right forGaucher Disease, Type 3 Shire 7