Not applicableStudy completedNCT00351156What this trial is testingStudy to Evaluate Blood Cell Lines From Patients With Gaucher DiseaseWho this might be right forGaucher Disease Amicus Therapeutics 50
Large-scale testing (Phase 3)Study completedNCT05529992What this trial is testingVelaglucerase Alfa (VPRIV) in Chinese Children, Teenagers, and Adults With Type 1 Gaucher DiseaseWho this might be right forGaucher Disease Takeda 20
Post-approval studies (Phase 4)Study completedNCT04120506What this trial is testingLong Term Impact of Rapid Intravenous Infusion of Velaglucerase Alfa (VPRIV)Who this might be right forGaucher Disease, Type 1 Shaare Zedek Medical Center 15
Post-approval studies (Phase 4)WithdrawnNCT03021941What this trial is testingPharmacokinetics, Pharmacodynamics And Safety Study Of Elelyso(tm) In Pediatric Subjects With Type 1 Gaucher DiseaseWho this might be right forType 1 Gaucher Disease Pfizer
Not applicableLooking for participantsNCT05253560What this trial is testingProdromal Parkinsonian Features in GBA1 Mutation CarriersWho this might be right forGaucher Disease, Type 1Healthy Shaare Zedek Medical Center 600
Testing effectiveness (Phase 2)Study completedNCT00391625What this trial is testingOpen-Label Extension Study Evaluating Long Term Safety in Patients With Type 1 Gaucher Disease Receiving DRX008A (ERT)Who this might be right forGaucher Disease Shire 10
Post-approval studies (Phase 4)Study completedNCT00365131What this trial is testingStudy of the Efficacy of Cerezyme in Testing Skeletal Disease in Patients With Type I Gaucher Disease.Who this might be right forGaucher Disease Type ICerebroside Lipidosis SyndromeClucocerebrosidase Deficiency Disease+2 more Genzyme, a Sanofi Company 40
Testing effectiveness (Phase 2)Study completedNCT00446550What this trial is testingOral AT2101 (Afegostat Tartrate) in Treatment-naive Patients With Gaucher DiseaseWho this might be right forGaucher DiseaseType 1 Gaucher DiseaseGaucher Disease, Type 1 Amicus Therapeutics 19
Not applicableStudy completedNCT01136304What this trial is testingValidating a New Severity Score System for Adults With Type 1 Gaucher Disease (GD1)Who this might be right forGaucher Disease University Research Foundation for Lysosomal Storage Diseases, Inc. 173
Large-scale testing (Phase 3)Study completedNCT02770625What this trial is testingPhase III Study of ISU302 in Patients With Type 1 Gaucher DiseaseWho this might be right forGaucher Disease, Type 1 ISU Abxis Co., Ltd. 8
Not applicableStudy completedNCT05687474What this trial is testingBaby Detect : Genomic Newborn ScreeningWho this might be right forCongenital Adrenal HyperplasiaFamilial Hyperinsulinemic Hypoglycemia 1Phosphoglucomutase 1 Deficiency+121 more Centre Hospitalier Universitaire de Liege 6,824
Testing effectiveness (Phase 2)UnknownNCT05447494What this trial is testingPhase 1/2 Study of CAN103 in Subjects With Gaucher DiseaseWho this might be right forGaucher Disease, Type 1Gaucher Disease, Type 3 CANbridge (Suzhou) Bio-pharma Co., Ltd. 40
Large-scale testing (Phase 3)WithdrawnNCT01161914What this trial is testingThe Safety and Efficacy Study of ISU302 in Patient With Type I Gaucher DiseaseWho this might be right forGaucher Disease ISU Abxis Co., Ltd.
Large-scale testing (Phase 3)Study completedNCT00635427What this trial is testingAn Open-Label Extension Study of GA-GCB ERT in Patients With Type 1 Gaucher DiseaseWho this might be right forGaucher Disease, Type 1 Shire 95
Very early researchActive Not RecruitingNCT06528080What this trial is testingA Clinical Study for the Treatment of Pediatric and Adolescent Patients With Type 1 Gaucher DiseaseWho this might be right forGaucher Disease Shanghai Jiao Tong University School of Medicine 3
Testing effectiveness (Phase 2)UnknownNCT06523517What this trial is testingEfficacy and Safety of Eliglustat in Chinese Pediatric Patients With Gaucher Disease Type 1 and Type 3Who this might be right forGaucher Disease Peking Union Medical College Hospital 5
Testing effectiveness (Phase 2)Active Not RecruitingNCT04411654What this trial is testingPhase 1/2 Clinical Trial of PR001 in Infants With Type 2 Gaucher Disease (PROVIDE)Who this might be right forGaucher Disease, Type 2 Prevail Therapeutics 7
Not applicableStudy completedNCT05702814What this trial is testingA Study Measuring Substances Potentially Indicating Bone Problems in Adults With Type 1 Gaucher ConditionWho this might be right forGaucher Disease Takeda 125
Large-scale testing (Phase 3)Study completedNCT00943111What this trial is testingEliglustat Tartrate (Genz-112638) in Patients With Gaucher Disease Who Have Reached Therapeutic Goals With Enzyme Replacement Therapy (ENCORE)Who this might be right forGaucher Disease, Type 1 Genzyme, a Sanofi Company 160
Not applicableStudy completedNCT02053896What this trial is testingA Switch-Over Study of the Safety and Efficacy of ISU302 in Patients With Type 1 Gaucher DiseaseWho this might be right forGaucher Disease ISU Abxis Co., Ltd. 5