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Results for “Gaucher Disease Type 3”

39 trials

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Showing 20 of 39 results

Testing effectiveness (Phase 2)Ended earlyNCT03746587
What this trial is testing

Study of Arimoclomol in Patients Diagnosed With Gaucher Disease Type 1 or 3

Who this might be right for
Gaucher Disease, Type 1Gaucher Disease, Type 3
ZevraDenmark 39
Not applicableStudy completedNCT00001289
What this trial is testing

Effects of Enzyme Replacement in Gaucher's Disease

Who this might be right for
Gaucher's Disease
National Institute of Neurological Disorders and Stroke (NINDS) 70
Large-scale testing (Phase 3)Not Yet RecruitingNCT07223944
What this trial is testing

A Gaucher Disease Gene Therapy Trial With FLT201

Who this might be right for
Gaucher Disease Type 1
Spur Therapeutics 45
Not applicableLooking for participantsNCT03240653
What this trial is testing

Gaucherite - A Study to Stratify Gaucher Disease

Who this might be right for
Gaucher Disease, Type IGaucher Disease, Type III
Cambridge University Hospitals NHS Foundation Trust 250
Large-scale testing (Phase 3)Study completedNCT01074944
What this trial is testing

Eliglustat Tartrate (Genz-112638) in Patients With Gaucher Disease to Evaluate Once Daily Versus Twice Daily Dosing (EDGE)

Who this might be right for
Gaucher Disease
Genzyme, a Sanofi Company 170
Not applicableLooking for participantsNCT05619900
What this trial is testing

Registry of Patients Diagnosed With Lysosomal Storage Diseases

Who this might be right for
Mucopolysaccharidosis IMucopolysaccharidosis IIMucopolysaccharidosis IV A+5 more
University of California, San Francisco 250
Large-scale testing (Phase 3)Study completedNCT00712348
What this trial is testing

Switchover Trial From Imiglucerase to Plant Cell Expressed Recombinant Human Glucocerebrosidase

Who this might be right for
Gaucher Disease
Pfizer 31
Early research (Phase 1)Looking for participantsNCT04532047
What this trial is testing

PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)

Who this might be right for
MPS IMPS IIMPS IVA+6 more
University of California, San Francisco 10
Not applicableActive Not RecruitingNCT07285369
What this trial is testing

High-Dose Ambroxol in Pediatric Type III Gaucher Disease (GD3)

Who this might be right for
Gaucher Disease, Type 3
Agyany Pharma LTD 12
Large-scale testing (Phase 3)Study completedNCT00943111
What this trial is testing

Eliglustat Tartrate (Genz-112638) in Patients With Gaucher Disease Who Have Reached Therapeutic Goals With Enzyme Replacement Therapy (ENCORE)

Who this might be right for
Gaucher Disease, Type 1
Genzyme, a Sanofi Company 160
Not applicableLooking for participantsNCT05586243
What this trial is testing

MAGNETIC RESONANCE SPECTROSCOPY BIOMARKERS IN TYPE 3 GAUCHER DISEASE (GD3)

Who this might be right for
Gaucher Disease, Type 3
University of Minnesota 5
Testing effectiveness (Phase 2)Active Not RecruitingNCT02843035
What this trial is testing

Venglustat in Combination With Cerezyme in Adult Patients With Gaucher Disease Type 3 With Venglustat Monotherapy Extension

Who this might be right for
Gaucher Disease Type 1Gaucher Disease Type 3
Genzyme, a Sanofi Company 12
Testing effectiveness (Phase 2)Not Yet RecruitingNCT06523517
What this trial is testing

Efficacy and Safety of Eliglustat in Chinese Pediatric Patients With Gaucher Disease Type 1 and Type 3

Who this might be right for
Gaucher Disease
Peking Union Medical College Hospital 5
Testing effectiveness (Phase 2)Active Not RecruitingNCT00911560
What this trial is testing

Bivalent Vaccine With Escalating Doses of the Immunological Adjuvant OPT-821, in Combination With Oral β-glucan for High-Risk Neuroblastoma

Who this might be right for
Neuroblastoma
Memorial Sloan Kettering Cancer Center 374
Not applicableUnknownNCT01274208
What this trial is testing

Examining the Immune Response in Patients With Gaucher Disease and Hepatitis C

Who this might be right for
Gaucher DiseaseHepatitis C
Shaare Zedek Medical Center 80
Testing effectiveness (Phase 2)Study completedNCT01685216
What this trial is testing

Efficacy and Safety Study of Velaglucerase Alfa in Children and Adolescents With Type 3 Gaucher Disease

Who this might be right for
Gaucher Disease, Type 3
Shire 7
Post-approval studies (Phase 4)Study completedNCT04120506
What this trial is testing

Long Term Impact of Rapid Intravenous Infusion of Velaglucerase Alfa (VPRIV)

Who this might be right for
Gaucher Disease, Type 1
Shaare Zedek Medical Center 15
Not applicableWithdrawnNCT00795197
What this trial is testing

A Screening Study Evaluating Disease Status of Gaucher Type I Patients

Who this might be right for
Gaucher Disease, Type 1
Genzyme, a Sanofi Company
Not applicableStudy completedNCT05687474
What this trial is testing

Baby Detect : Genomic Newborn Screening

Who this might be right for
Congenital Adrenal HyperplasiaFamilial Hyperinsulinemic Hypoglycemia 1Phosphoglucomutase 1 Deficiency+121 more
Centre Hospitalier Universitaire de Liege 6,824
Large-scale testing (Phase 3)Study completedNCT00891202
What this trial is testing

Eliglustat Tartrate (Genz-112638) in Patients With Gaucher Disease (ENGAGE)

Who this might be right for
Gaucher Disease, Type 1
Genzyme, a Sanofi Company 40
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