Testing effectiveness (Phase 2)Study completedNCT01712204What this trial is testingA Proof-of-Concept Study of AC-201 to Prevent Gout FlaresWho this might be right forGout Flares TWi Biotechnology, Inc. 82
Not applicableStudy completedNCT02320084What this trial is testingLong Term Safety Study of Orfadin Treatment in HT-1 Patients in Standard Clinical CareWho this might be right forHereditary Tyrosinemia, Type I Swedish Orphan Biovitrum 315
Testing effectiveness (Phase 2)Study completedNCT01565616What this trial is testingBone Marrow Transplantation in Young Adults With Severe Sickle Cell DiseaseWho this might be right forSickle Cell Disease Emory University 22
Large-scale testing (Phase 3)Study completedNCT00599326What this trial is testingPilot Trial of Deferasirox in the Treatment of Porphyria Cutanea TardaWho this might be right forPorphyria Cutanea Tarda University of Texas Southwestern Medical Center 10
Large-scale testing (Phase 3)Not Yet RecruitingNCT07318363What this trial is testingIGNITE-TX Phase III: (Identifying Individuals for Genetic Testing & Treatment) InterventionWho this might be right forCommunicationInformed Decision-making M.D. Anderson Cancer Center 2,100
Large-scale testing (Phase 3)Study completedNCT01580293What this trial is testingA Trial Investigating Safety and Efficacy of Treatment With BAY94-9027 in Severe Hemophilia AWho this might be right forHemophilia A Bayer 145
Early research (Phase 1)Study completedNCT00002321What this trial is testingA Phase I Study of the Safety of Proleukin (Aldesleukin) in Combination With Ganciclovir and Antiretroviral Therapy in HIV Seropositive Patients With Cytomegalovirus (CMV) RetinitisWho this might be right forCytomegalovirus RetinitisHIV Infections Chiron Corporation
Large-scale testing (Phase 3)Study completedNCT00214604What this trial is testingType III DysbetalipoproteinemiaWho this might be right forHyperlipoproteinemia Type III AstraZeneca 30
Large-scale testing (Phase 3)Study completedNCT00449878What this trial is testingLiprotamase Efficacy Trial in Patients With Cystic Fibrosis-Related Exocrine Pancreatic InsufficiencyWho this might be right forCystic FibrosisExocrine Pancreatic Insufficiency Anthera Pharmaceuticals 163
Not applicableLooking for participantsNCT07363304What this trial is testingImpact of Elexacaftor-Tezacaftor-Ivacaftor Treatment on Metabolic, Epigenetic and Fecal Microbiota Profiles in People With Cystic Fibrosis.Who this might be right forCystic Fibrosis (CF) Meyer Children's Hospital IRCCS 150
Not applicableStudy completedNCT01878604What this trial is testingGene Analysis and Treatment Optimization in Chinese Homozygous Familial HypercholesterolemiaWho this might be right forHomozygous Familial Hypercholesterolemia Central South University 5
Post-approval studies (Phase 4)Study completedNCT00119158What this trial is testingCombination Therapy for Atopic DermatitisWho this might be right forAtopic Dermatitis Children's Hospital of Philadelphia 90
Not applicableStudy completedNCT01428258What this trial is testingPhase 2 Study of Glycomacropeptide Versus Amino Acid Diet for Management of PhenylketonuriaWho this might be right forPhenylketonuria University of Wisconsin, Madison 32
Large-scale testing (Phase 3)Study completedNCT03355209What this trial is testingInvestigate the Efficacy and Safety of ZX008 (Fenfluramine Hydrochloride) as an Adjunctive Therapy in Children and Adults With Lennox-Gastaut SyndromeWho this might be right forLennox Gastaut Syndrome Zogenix International Limited, Inc., a subsidiary of Zogenix, Inc. 296
Not applicableStudy completedNCT04595578What this trial is testingCerebellar rTMS and Physical Therapy for Cerebellar AtaxiaWho this might be right forMultiple System Atrophy, Cerebellar Variant (Disorder)Spinocerebellar Ataxias Samsung Medical Center 34
Testing effectiveness (Phase 2)Study completedNCT02247206What this trial is testingVoIP Delivered Behavior Therapy for Tourette SyndromeWho this might be right forTourette SyndromeChronic Tic Disorder University of Wisconsin, Milwaukee 20
Not applicableStudy completedNCT03534609What this trial is testingLutronic Genius System for Neck TreatmentWho this might be right forWrinkleSkin LaxitySkin Texture Disorder CynosureLutronic 18
Not applicableStudy completedNCT01329198What this trial is testingBrain Stimulation for the Treatment of Tourette SyndromeWho this might be right forTourette Syndrome University of Florida 5
Post-approval studies (Phase 4)Study completedNCT01419249What this trial is testingFirst Year Growth Response Associated Genetic Markers Validation Phase IV Open-label Study in Growth Hormone Deficient and Turner Syndrome Pre-pubertal Children: the PREDICT Pharmacogenetics Validation StudyWho this might be right forIdiopathic Growth Hormone DeficiencyTurner Syndrome Merck KGaA, Darmstadt, Germany 458
Early research (Phase 1)Study completedNCT01642485What this trial is testingFood and Insulin Effect on QT/QTC Interval of ECGWho this might be right forEffects of Different Meals on the QT/QTc IntervalInsulin and Oral Hypoglycemic [Antidiabetic] Drugs Causing Adverse Effects in Therapeutic UseC-Peptide Effects on the QT/QTc Interval+2 more Richmond Pharmacology Limited 32