Not applicableStudy completedNCT01568879What this trial is testingEvaluating the Effectiveness of a Chronic Disease Management Program for GoutWho this might be right forRecurrent or Tophaceous Gout Kaiser Permanente 104
Large-scale testing (Phase 3)Study completedNCT05033080What this trial is testingVX-121 Combination Therapy in Participants With Cystic Fibrosis (CF) Heterozygous for F508del and a Minimal Function Mutation (F/MF)Who this might be right forCystic Fibrosis Vertex Pharmaceuticals Incorporated 435
Testing effectiveness (Phase 2)Ended earlyNCT00079859What this trial is testingImplitapide in Patients With Heterozygous Familial Hypercholesterolemia (HeFH) on Maximal Concurrent Lipid-Lowering TherapyWho this might be right forFamilial Hypercholesterolemia Medical Research Laboratories International 120
Not applicableStudy completedNCT02207218What this trial is testingTo Investigate Safety and Efficacy of NovoEight® (rFVIII) During Long-term Treatment of Haemophilia A in JapanWho this might be right forCongenital Bleeding DisorderHaemophilia A Novo Nordisk A/S 40
Not applicableUnknownNCT02433782What this trial is testingMyofascial Therapy in Patients With Hemophilic ArthropathyWho this might be right forHemophilia Universidad Católica San Antonio de Murcia 25
Not applicableUnknownNCT04803474What this trial is testingTurner And Klinefelter Treatment Target StudyWho this might be right forKlinefelter SyndromeTurner Syndrome dr. Laura C. G. de Graaff-Herder 370
Not applicableStudy completedNCT00148746What this trial is testingStandardized Time- and Score-oriented Treatment of Moderate and Severe Atopic DermatitisWho this might be right forModerate to Severe Atopic Dermatitis Technische Universität Dresden
Testing effectiveness (Phase 2)Study completedNCT02047318What this trial is testingAn Extension Study to Evaluate the Long-Term Safety and Durability of Effect of LUM001 in the Treatment of Cholestatic Liver Disease in Subjects With Alagille Syndrome (ALGS)Who this might be right forAlagille Syndrome Mirum Pharmaceuticals, Inc. 19
Not applicableUnknownNCT05295524What this trial is testingDescription of the Short-term Effects of KAFTRIO® by Continuous Monitoring With the PHEAL-CR-K Application in Real Life in Patients With Cystic Fibrosis Eligible for KAFTRIO® TreatmentWho this might be right forCystic Fibrosis Hopital Foch 50
Post-approval studies (Phase 4)Study completedNCT05458479What this trial is testingFluoxetine Treatment of Depression in Down SyndromeWho this might be right forDown SyndromeDepression Massachusetts General Hospital 4
Post-approval studies (Phase 4)Study completedNCT04985682What this trial is testingADVATE in People With Hemophilia A in IndiaWho this might be right forHemophilia A Baxalta now part of Shire 50
Not applicableStudy completedNCT00328159What this trial is testingNutritional Therapy of the Deficits of Oxidation Mitochondrial of the Fatty AcidsWho this might be right forInborn Errors of Metabolism Assistance Publique - Hôpitaux de Paris 20
Testing effectiveness (Phase 2)Study completedNCT00043342What this trial is testingStudy of Interferon Gamma-1b by Injection for the Treatment of Patients With Cystic FibrosisWho this might be right forCystic Fibrosis InterMune 51
Not applicableStudy completedNCT03183934What this trial is testingA Follow-up Study to Evaluate the Efficacy and Safety of ALLO-ASC-DFU in ALLO-ASC-EB-101 Clinical TrialWho this might be right forDystrophic Epidermolysis Bullosa Anterogen Co., Ltd. 2
Large-scale testing (Phase 3)Study completedNCT06153784What this trial is testingThalidomide and Hydroxyurea Combination in β-Thalassemia PatientsWho this might be right forThalassemia, Beta Children's Hospital Karachi 603
Not applicableUnknownNCT05601557What this trial is testingResearch on the Clinical Characteristics and Key Diagnosis and Treatment Technology of Genetic and Metabolic Liver DiseaseWho this might be right forDiagnosis ， Treatment， Genetic and Metabolic Liver Disease Sujun Zheng 480
Testing effectiveness (Phase 2)Study completedNCT03921528What this trial is testingAn Active Treatment Study of SRK-015 in Patients With Type 2 or Type 3 Spinal Muscular AtrophyWho this might be right forSpinal Muscular AtrophySpinal Muscular Atrophy Type 3Spinal Muscular Atrophy Type 2+6 more Scholar Rock, Inc. 58
Large-scale testing (Phase 3)Study completedNCT01270971What this trial is testingEfficacy and Safety Evaluation of AN2690 Topical Solution to Treat Onychomycosis of the ToenailWho this might be right forOnychomycosis of Toenails Pfizer 594
Not applicableUnknownNCT05857709What this trial is testingFitness, Body Composition, Physical Activity and Sleep Patterns in People With Cystic Fibrosis on Modulator Therapy.Who this might be right forCystic Fibrosis University of Portsmouth 100
Testing effectiveness (Phase 2)Study completedNCT03240133What this trial is testingStudy of BCX7353 as a Treatment for Attacks of Hereditary AngioedemaWho this might be right forHereditary Angioedema (HAE) BioCryst Pharmaceuticals 58