Not applicableLooking for participantsNCT03190837What this trial is testingA Long-term Follow-up Study of Gaucher DiseaseWho this might be right forGaucher Disease Duke University 200
Early research (Phase 1)Study completedNCT01381445What this trial is testingA Study Assessing GW870086's Potential to Cause Skin ThinningWho this might be right forDermatitis, Atopic GlaxoSmithKline 20
Testing effectiveness (Phase 2)Study completedNCT00577577What this trial is testingSafety and Efficacy Study of Recombinant Human Insulin-Like Growth Factor-I/Recombinant Human Insulin-Like Growth Factor Binding Protein-3 (rhIGF-I/rhIGFBP-3) In Myotonic Dystrophy Type 1Who this might be right forMyotonic Dystrophy Type 1 Insmed Incorporated 69
Not applicableUnknownNCT02709057What this trial is testingLifestyle Intervention in Individuals With Low or High Genetic Risk for Type 2 DiabetesWho this might be right forType 2 Diabetes University of Eastern Finland 1,200
Early research (Phase 1)Study completedNCT04926701What this trial is testingA First in Human Study to Evaluate the Safety, Tolerability and Pharmacokinetics of Single and Multiple Ascending Doses of Inhaled ETD001 in Healthy SubjectsWho this might be right forCystic Fibrosis Enterprise Therapeutics Ltd 98
Not applicableUnknownNCT06714019What this trial is testingPL_GNT01_ISR_Grant 53234273Who this might be right forTransthyretin Cardiomyopathy (TTR-CM)Transthyretin (TTR) Amyloid CardiomyopathyTransthyretin Amyloidosis National Institute of Cardiology, Warsaw, Poland 100
Not applicableLooking for participantsNCT06970028What this trial is testingSomatosensory Phenotyping of ADPKDWho this might be right forADPKDPain Universitaire Ziekenhuizen KU Leuven 150
Not applicableLooking for participantsNCT07286565What this trial is testingActive NBS Study: Decentralised Monitoring Motor Development in Children With Duchenne Muscular Dystrophy or Spinal Muscular Atrophy Identified by Newborn ScreeningWho this might be right forSpinal Muscular Atrophy (SMA)Duchenne Muscular Dystrophy (DMD) Centre Hospitalier Universitaire de Liege 100
Not applicableStudy completedNCT00579267What this trial is testingReliability and Validity of the MINI International Neuropsychiatric Interview for Children and Adolescents (MINI-KID)Who this might be right forMajor DepressionManiaAnxiety Disorders+11 more University of South Florida 230
Testing effectiveness (Phase 2)Study completedNCT01733407What this trial is testingL-Serine Supplementation in Hereditary Sensory Neuropathy Type 1Who this might be right forHereditary Sensory and Autonomic Neuropathy Type I Massachusetts General Hospital 18
Testing effectiveness (Phase 2)Active Not RecruitingNCT01736592What this trial is testingPhase I/II Follow-up Study of SAR422459 in Patients With Stargardt's Macular DegenerationWho this might be right forStargardt's Disease Sanofi 27
Not applicableStudy completedNCT07565636What this trial is testing3D Printed Orthosis for Wrist Instability for Ehlers-Danlos Syndrome PatientWho this might be right forEhlers-Danlos Syndrome Hypermobility Type (hEDS) ELewis 2
Not applicableStudy completedNCT00005111What this trial is testingPET Scans in Normal Volunteers and Patients With Fabry DiseaseWho this might be right forFabry DiseaseHealthy National Institute of Neurological Disorders and Stroke (NINDS) 24
Not applicableStudy completedNCT03317171What this trial is testingSafety and Efficacy of a Flavonoids- and omega3s-based Compound for the Treatment of Muscular DystrophiesWho this might be right forMuscular DystrophiesMuscle Inflammation Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico 29
Not applicableUnknownNCT02062671What this trial is testingRenal Sympathetic Denervation for Reduction of Pain and Improvement of Insulin Sensitivity in Adult Polycystic Kidney DiseaseWho this might be right forAdult Polycystic Kidney Disease Odense University Hospital 12
Testing effectiveness (Phase 2)WithdrawnNCT06087731What this trial is testingEfficacy and Safety of Tocilizumab for TAOWho this might be right forTocilizumabThyroid Associated Ophthalmopathy Sun Yat-sen University
Not applicableWithdrawnNCT03207230What this trial is testingMulticenter Exploratory Study of Accelerometry in Dilated CardiomyopathyWho this might be right forDilated Cardiomyopathy Stanford University
Large-scale testing (Phase 3)Ended earlyNCT00404300What this trial is testingOptivate in People With Von Willebrand Disease Undergoing SurgeryWho this might be right forVon Willebrand Disease Bio Products Laboratory 25
Early research (Phase 1)Study completedNCT06219902What this trial is testingLearn if Elinzanetant Affects the Ability to Drive and Brain Function in Healthy WomenWho this might be right forVasomotor Symptoms as a Sex Hormone-dependent Disorder in Women and MenHot Flashes Bayer 64
Large-scale testing (Phase 3)Study completedNCT00662675What this trial is testingThe Efficacy and Tolerability of Pancrelipase Microtablet (MT) Capsules for the Treatment of Cystic Fibrosis-dependent Exocrine Pancreatic InsufficiencyWho this might be right forExocrine Pancreatic InsufficiencySteatorrheaMalabsorption Syndromes+1 more Johnson & Johnson Pharmaceutical Research & Development, L.L.C. 40