Testing effectiveness (Phase 2)Study completedNCT02931071
What this trial is testing
Clinical Phase II Trial to Evaluate CD34+ Cells Mobilization and Collection in Patients With Fanconi Anemia for Subsequent Transduction With a Lentiviral Vector Carring FANCA Gene. FANCOSTEM-1
Who this might be right for
Fanconi Anemia
Hospital Universitari Vall d'Hebron Research Institute 13