Testing effectiveness (Phase 2)Study completedNCT02974855What this trial is testingPF-06741086 Multiple Dose Study in Severe HemophiliaWho this might be right forHemophilia A or B Pfizer 27
Testing effectiveness (Phase 2)Study completedNCT00951405What this trial is testingSafety and Efficacy of 3 Different Doses of Long Acting Factor VII in Haemophilia A or B Patients With InhibitorsWho this might be right forCongenital Bleeding DisorderHaemophilia A With InhibitorsHaemophilia B With Inhibitors Novo Nordisk A/S 23
Large-scale testing (Phase 3)Active Not RecruitingNCT03861273What this trial is testingEvaluate the Efficacy and Safety of Factor IX Gene Therapy With PF-06838435 in Adult Males With Moderately Severe to Severe Hemophilia BWho this might be right forHemophilia B Pfizer 51
Not applicableStudy completedNCT02061072What this trial is testingWeb-based Application for the Population Pharmacokinetic Service - Phase 1Who this might be right forHemophilia AHemophilia B McMaster University 400
Large-scale testing (Phase 3)Study completedNCT01488994What this trial is testingBAX 326 Pediatric StudyWho this might be right forHemophilia B Baxalta now part of Shire 23
Early research (Phase 1)Study completedNCT02035605What this trial is testingAn Investigational Drug, ALN-AT3SC, in Healthy Volunteers and Hemophilia A or B PatientsWho this might be right forHemophilia AHemophilia B Sanofi 51
Testing effectiveness (Phase 2)Ended earlyNCT05789524What this trial is testingThe Efficacy and Safety of SerpinPC in Participants with Severe Hemophilia a or Moderately Severe to Severe Hemophilia BWho this might be right forHemophilia aHemophilia B ApcinteX Ltd 60
Not applicableStudy completedNCT03055611What this trial is testingEvaluate the Real-world Usage and Effectiveness of Elocta and Alprolix in Patients With Haemophilia A or BWho this might be right forHaemophilia AHaemophilia B Swedish Orphan Biovitrum 201
Early research (Phase 1)Study completedNCT01563471What this trial is testingSafety and Tolerability of Intravenous Doses of Activated Recombinant Human Factor VII in Healthy VolunteersWho this might be right forCongenital Bleeding DisorderHaemophilia A With InhibitorsHaemophilia B With Inhibitors+1 more Novo Nordisk A/S 39
Testing effectiveness (Phase 2)Study completedNCT02541942What this trial is testingPharmacogenetic Testing of Saliva Samples From Patients With Five or More Exposure Days to rFVIIa Analogue in the Adept™2 TrialWho this might be right forCongenital Bleeding DisorderHaemophilia A With InhibitorsHaemophilia B With Inhibitors Novo Nordisk A/S 19
Not applicableLooking for participantsNCT06147414What this trial is testingDevelopment of Non-Invasive Prenatal Diagnosis for Single Gene DisordersWho this might be right forInvasive PreNatal Diagnosis in a Context of Family History of Single-gene Disorders, IncludingSickle Cell DiseaseCystic Fibrosis+12 more Assistance Publique - Hôpitaux de Paris 550
Not applicableStudy completedNCT02776826What this trial is testingWorld Bleeding Disorders Registry Pilot StudyWho this might be right forHemophilia A and B World Federation of Hemophilia 356
Not applicableLooking for participantsNCT02979119What this trial is testingThe European Paediatric Network for Haemophilia Management ( PedNet Registry)Who this might be right forFactor VIII DeficiencyFactor IX Deficiency PedNet Haemophilia Research Foundation 4,000
Large-scale testing (Phase 3)Active Not RecruitingNCT04082429What this trial is testingResearch Study to Look at How Well the Drug Concizumab Works in Your Body if You Have Haemophilia Without InhibitorsWho this might be right forHaemophilia A Without InhibitorsHaemophilia B Without Inhibitors Novo Nordisk A/S 156
Early research (Phase 1)WithdrawnNCT03996486What this trial is testingStudy to Test the Safety of an Investigational Drug Given Repeatedly to Adult Men With Severe HemophiliaWho this might be right forHemophilia Bayer
Early research (Phase 1)Study completedNCT03481946What this trial is testingAssess Pharmacokinetics and Pharmacodynamics Following Administration of BAY1093884 in Patients With Severe HemophiliaWho this might be right forHemophilia A; Hemophilia B Bayer 6
Not applicableEnded earlyNCT01460147What this trial is testingOsteoporosis and MRI Study in HemophiliaWho this might be right forBone Mineral DensityHemophilia AHemophilia B Baxalta now part of Shire 3
Testing effectiveness (Phase 2)Ended earlyNCT00947193What this trial is testingStudy of Ataluren (PTC124) in Hemophilia A and BWho this might be right forHemophilia AHemophilia B PTC Therapeutics 13
Not applicableActive Not RecruitingNCT03655223What this trial is testingEarly Check: Expanded Screening in NewbornsWho this might be right forSpinal Muscular AtrophyFragile X SyndromeFragile X - Premutation+182 more RTI International 30,000
Large-scale testing (Phase 3)Study completedNCT02020369What this trial is testingPhase III Study of Coagulation FVIIa (Recombinant) in Congenital Hemophilia A or B Patients With InhibitorsWho this might be right forHemophilia A With InhibitorsHemophilia B With Inhibitors rEVO Biologics 27