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Results for “Hemoglobinuria, Paroxysmal Nocturnal (PNH)”

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Showing 10 of 0 results

Testing effectiveness (Phase 2)Study completedNCT03896152
What this trial is testing

Efficacy, Safety, Pharmacokinetics and Pharmacodynamics Study, Assessing Multiple LNP023 Doses in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Novartis Pharmaceuticals 13
Testing effectiveness (Phase 2)Ended earlyNCT05116787
What this trial is testing

BCX9930 for the Treatment of Paroxysmal Nocturnal Hemoglobinuria (PNH) in Participants Not Receiving Other Complement Inhibitor Therapy

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria (PNH)
BioCryst Pharmaceuticals 12
Not applicableStudy completedNCT01272817
What this trial is testing

Nonmyeloablative Allogeneic Transplant

Who this might be right for
Aplastic AnemiaParoxysmal Nocturnal HemoglobinuriaAcute Myelogenous Leukemia+15 more
Scripps Health 36
Large-scale testing (Phase 3)Looking for participantsNCT06932471
What this trial is testing

Study of Safety and Efficacy of MY008211A in Patients With Residual Anemia Despite Anti-C5 Antibody Treatment

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Wuhan Createrna Science and Technology Co., Ltd 20
Testing effectiveness (Phase 2)Active Not RecruitingNCT05476887
What this trial is testing

To Evaluate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Efficacy of KP104

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Kira Pharmacenticals (US), LLC. 35
Not applicableLooking for participantsNCT06931691
What this trial is testing

A Multi-center, Ambispective Cohort Study to Evaluate the Impact of Iptacopan for Adult Patients With PNH in China

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Novartis Pharmaceuticals 80
Large-scale testing (Phase 3)Study completedNCT06578949
What this trial is testing

Efficacy, Safety, Pharmacokinetics, Pharmacodynamics, and Immunogenicity of Ravulizumab in Chinese Adults Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH)

Who this might be right for
Paroxysmal Nocturnal HemoglobinuriaPNH
Alexion Pharmaceuticals, Inc. 18
Early research (Phase 1)Study completedNCT06100900
What this trial is testing

Dose Escalation of BCX10013 in Participants with Paroxysmal Nocturnal Hemoglobinuria (PNH)

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
BioCryst Pharmaceuticals 8
Testing effectiveness (Phase 2)Study completedNCT02534909
What this trial is testing

Proof of Concept Study to Assess the Efficacy, Safety and Pharmacokinetics of LFG316 in Patients With Paroxysmal Nocturnal Hemoglobinuria

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Novartis Pharmaceuticals 10
Testing effectiveness (Phase 2)Looking for participantsNCT04901936
What this trial is testing

Pegcetacoplan in Pediatric Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria (PNH)Paroxysmal Hemoglobinuria
Apellis Pharmaceuticals, Inc. 12