Early research (Phase 1)Ended earlyNCT01620801What this trial is testingHemophilia B Gene Therapy With AAV8 VectorWho this might be right forHemophilia B Spark Therapeutics, Inc. 4
Large-scale testing (Phase 3)Study completedNCT03938792What this trial is testingStudy of the Efficacy and Safety PF-06741086 in Adult and Teenage Participants With Severe Hemophilia A or Moderately Severe to Severe Hemophilia BWho this might be right forHemophilia AHemophilia B Pfizer 189
Not applicableStudy completedNCT00195221What this trial is testingStudy to Describe the Allergic Reactions to Factor IX in Patients With Hemophilia BWho this might be right forHemophilia BAllergic Reactions Wyeth is now a wholly owned subsidiary of Pfizer 166
Not applicableStudy completedNCT05617209What this trial is testingIn Vitro Correction of Thrombin Generation by Concizumab (Anti-TFPI) for Severe Hemophilia PatientsWho this might be right forHemophilia Centre Hospitalier Universitaire de Saint Etienne 20
Not applicableStudy completedNCT00936312What this trial is testingFemales With Severe or Moderate Hemophilia A or B: an International Multi-center StudyWho this might be right forHemophilia AHemophilia B Weill Medical College of Cornell University 200
Large-scale testing (Phase 3)Study completedNCT02250560What this trial is testingInvestigate the Safety and Efficacy of Replenine®-VF in Haemophilia B Patients Undergoing Major Surgery.Who this might be right forHaemophilia B Bio Products Laboratory
Not applicableEnrolling By InvitationNCT03655223What this trial is testingEarly Check: Expanded Screening in NewbornsWho this might be right forSpinal Muscular AtrophyFragile X SyndromeFragile X - Premutation+182 more RTI International 30,000
Not applicableWithdrawnNCT04541875What this trial is testingMedication Adherence and Non-adherence in Adults With Rare DiseaseWho this might be right forCystic FibrosisHemophilia AHemophilia B+3 more Xperiome
Large-scale testing (Phase 3)Study completedNCT01286779What this trial is testingBAX 326 (rFIX) Continuation StudyWho this might be right forHemophilia B Baxalta now part of Shire 117
Large-scale testing (Phase 3)Study completedNCT01425723What this trial is testingLong-Term Safety and Efficacy of rFIXFc in the Prevention and Treatment of Bleeding Episodes in Previously Treated Participants With Hemophilia BWho this might be right forSevere Hemophilia B Bioverativ Therapeutics Inc. 120
Testing effectiveness (Phase 2)Looking for participantsNCT06379789What this trial is testingInvestigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia BWho this might be right forHemophilia B Regeneron Pharmaceuticals 130
Not applicableStudy completedNCT04590950What this trial is testingDosage and PD Study of Eftrenonacog-alfaWho this might be right forSevere Haemophilia B Assistance Publique - Hôpitaux de Paris 15
Not applicableStudy completedNCT02971969What this trial is testingLong-Term Safety, Tolerability, and Efficacy of DTX101 (AAVrh10FIX) in Adults With Moderate/Severe to Severe Hemophilia BWho this might be right forHemophilia B Ultragenyx Pharmaceutical Inc 6
Testing effectiveness (Phase 2)Study completedNCT03370172What this trial is testingBAX 888 in Male Adults With Severe Hemophilia AWho this might be right forHemophilia A Baxalta now part of Shire 4
Post-approval studies (Phase 4)UnknownNCT04534751What this trial is testingFactor In the Initial Resuscitation of Severe Trauma 2 PatientsWho this might be right forTraumatic HemorrhageCoagulopathyMassive Hemorrhage University Health Network, Toronto 350
Post-approval studies (Phase 4)Study completedNCT00638001What this trial is testingImpact of Conservative Treatment by Custom-made Orthoses in Patients With Haemophilic Ankle ArthropathyWho this might be right forHaemophilia AHaemophilia B Cliniques universitaires Saint-Luc- Université Catholique de Louvain 70
Large-scale testing (Phase 3)Study completedNCT00093210What this trial is testingStudy Evaluating of Recombinant Human Factor IX (BeneFIX) and a New Formulation of BeneFIX (rFIX-R) in Moderate to Severe Hemophilia BWho this might be right forHemophilia B Wyeth is now a wholly owned subsidiary of Pfizer
Testing effectiveness (Phase 2)Study completedNCT01361126What this trial is testingA Safety and Efficacy Study of a Recombinant Factor IX in Patients With Severe Hemophilia BWho this might be right forHemophilia B CSL Behring 17
Post-approval studies (Phase 4)Study completedNCT00092976What this trial is testingStudy Evaluating ReFacto® in Hemophilia A Undergoing Major SurgeryWho this might be right forHemophilia A Wyeth is now a wholly owned subsidiary of Pfizer 15
Large-scale testing (Phase 3)Study completedNCT03587116What this trial is testingEvaluate Prospective Efficacy and Safety Data of Current FIX Prophylaxis Replacement Therapy in Adult Hemophilia B Subjects (FIX:C≤2%) or Current FVIII Prophylaxis Replacement Therapy in Adult Hemophilia A Subjects (FVIII:C≤1%)Who this might be right forHemophilia BHemophilia A Pfizer 212