Post-approval studies (Phase 4)Looking for participantsNCT05412394What this trial is testingOnce Weekly Infant Corticosteroid Trial for DMDWho this might be right forDuchenne Muscular Dystrophy Anne M. Connolly 26
Not applicableStudy completedNCT02118779What this trial is testingObservational Prolonged Trial in Myotonic Dystrophy Type 1Who this might be right forMyotonic Dystrophy Type 1 Radboud University Medical Center 255
Not applicableNot Yet RecruitingNCT07369609What this trial is testingFactors Influencing Physical Activity Levels in Children With Duchenne Muscular Dystrophy: An ICF-CY-Based StudyWho this might be right forDuchenne Muscular Dystrophy (DMD) Hacettepe University 30
Testing effectiveness (Phase 2)Study completedNCT04179409What this trial is testingA 48-Week, Open Label, Study to Evaluate the Efficacy and Safety of AMONDYS 45, EXONDYS 51, VYONDYS 53 in Subjects With DuchenneMuscular Dystrophy Carrying Eligible DMD Duplications.Who this might be right forDuchenne Muscular Dystrophy Kevin Flanigan 3
Large-scale testing (Phase 3)Study completedNCT03692312What this trial is testingEfficacy and Safety of Tideglusib in Congenital Myotonic DystrophyWho this might be right forCongenital Myotonic Dystrophy AMO Pharma Limited 56
Not applicableActive Not RecruitingNCT01671865What this trial is testingMagnetic Resonance Imaging and Spectroscopy Biomarkers for Facioscapulohumeral Muscular DystrophyWho this might be right forFacioscapulohumeral Muscular Dystrophy Hugo W. Moser Research Institute at Kennedy Krieger, Inc. 75
Testing effectiveness (Phase 2)Ended earlyNCT04004065What this trial is testingTwo-Part Study for Dose Determination of Vesleteplirsen (SRP-5051) (Part A), Then Dose Expansion (Part B) in Participants With Duchenne Muscular Dystrophy Amenable to Exon 51-Skipping TreatmentWho this might be right forDuchenne Muscular Dystrophy Sarepta Therapeutics, Inc. 62
Very early researchLooking for participantsNCT07188012What this trial is testingSafety and Dystrophin Expression of SPOT-03 in Duchenne Muscular Dystrophy (DMD) PatientsWho this might be right forDuchenne Muscular Dystrophy (DMD) Shanghai Siponuoyin Biotechnology Co Ltd 9
Large-scale testing (Phase 3)Study completedNCT02147639What this trial is testingEffects of Sodium Nitrate on Blood Flow in Becker Muscular DystrophyWho this might be right forBecker Muscular Dystrophy Cedars-Sinai Medical Center 19
Not applicableUnknownNCT03611244What this trial is testingPrevention of Scoliosis in Patients With Duchenne Muscular Dystrophy Using Portable Seat DeviceWho this might be right forScoliosis NeuromuscularDuchenne Muscular DystrophyLordosis Lumbar Seoul National University Hospital 98
Not applicableStudy completedNCT00457912What this trial is testingGenetic Characterization of Individuals With Limb Girdle Muscular DystrophyWho this might be right forLimb-Girdle Muscular Dystrophy Nationwide Children's Hospital 277
Not applicableUnknownNCT04139460What this trial is testingCRT-P or CRT-D in Dilated CardiomyopathyWho this might be right forCardiomyopathy, Dilated, 3B University Hospital Olomouc 924
Not applicableStudy completedNCT02876809What this trial is testingA Model for Healthy Aging: Moscow Centenarians (AGE-100)Who this might be right forAging Pirogov Russian National Research Medical University 100
Not applicableStudy completedNCT03127241What this trial is testingUser-centred Assistive System for Arm Functions in Neuromuscular SubjectsWho this might be right forMuscular DystrophiesMuscular Dystrophy, DuchenneMuscular Dystrophy, Becker+1 more Politecnico di Milano 38
Not applicableStudy completedNCT04313595What this trial is testingDevice for Breathing Frequency Monitoring in Muscular DystrophyWho this might be right forMuscular Dystrophies IRCCS Eugenio Medea 15
Not applicableApproved For MarketingNCT02592941What this trial is testingDeflazacort Expanded Access Program for Children, Adolescents and Adults With Duchenne Muscular DystrophyWho this might be right forDuchenne Muscular Dystrophy PTC Therapeutics
Early research (Phase 1)Study completedNCT03627494What this trial is testingFirst Time in Human (FTIH) Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Single and Repeat Doses of GSK3439171A in Healthy Subjects and to Assess Food EffectWho this might be right forMuscular Dystrophies GlaxoSmithKline 66
Testing effectiveness (Phase 2)UnknownNCT01834066What this trial is testingStudy Safety and Efficacy of Bone Marrow Derived Autologous Cells for the Treatment of Muscular Dystrophy.Who this might be right forMuscular DystrophyDuchenne Muscular Dystrophy, Chaitanya Hospital, Pune 25
Not applicableEnrolling By InvitationNCT06412328What this trial is testingPsychoeducation Program for Parents of Children with Duchenne Muscular DystrophyWho this might be right forPsychoeducationParentsPsychological Wellness+1 more Lokman Hekim University 26
Not applicableApproved For MarketingNCT04337112What this trial is testingThe Expanded Access Use of Viltolarsen in Duchenne Muscular Dystrophy With Confirmed Exon 53 Amenable MutationWho this might be right forMuscular Dystrophy, DuchenneDMD NS Pharma, Inc.