Not applicableStudy completedNCT04202627What this trial is testingBiomarker Development in LGMD2iWho this might be right forMuscular DystrophiesLimb Girdle Muscular Dystrophy ML Bio Solutions, Inc. 101
Testing effectiveness (Phase 2)Study completedNCT00264888What this trial is testingSafety and Efficacy Study of PTC124 in Duchenne Muscular DystrophyWho this might be right forDuchenne Muscular Dystrophy PTC Therapeutics 38
Testing effectiveness (Phase 2)Looking for participantsNCT06138639What this trial is testingSGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)Who this might be right forDuchenne Muscular Dystrophy Solid Biosciences Inc. 60
Early research (Phase 1)WithdrawnNCT02050776What this trial is testingStem Cell Therapy in Limb Girdle Muscular DystrophyWho this might be right forLimb Girdle Muscular Dystrophy Neurogen Brain and Spine Institute
Very early researchEnded earlyNCT02653833What this trial is testingThe Study of Skeletal Muscle Blood Flow in Becker Muscular DystrophyWho this might be right forMuscular Dystrophy Cedars-Sinai Medical Center 6
Post-approval studies (Phase 4)Study completedNCT01422200What this trial is testingFlu Vaccine Study in Neuromuscular Patients 2011Who this might be right forDuchenne Muscular DystrophySpinal Muscular AtrophyCongenital Muscular Dystrophy Children's Hospital Medical Center, Cincinnati 22
Not applicableStudy completedNCT03521271What this trial is testingInvestigation Of Factors Affecting Hand Functions in Nonambulatory Patients With Duchenne Muscular DystrophyWho this might be right forDuchenne Muscular Dystrophy Hacettepe University 23
Early research (Phase 1)Study completedNCT02235844What this trial is testingAllogeneic Human Umbilical Cord Mesenchymal Stem Cells for a Single Male Patient With Duchenne Muscular Dystrophy (DMD)Who this might be right forDuchenne's Muscular Dystrophy Allergy and Asthma Consultants, Wichita, Kansas 1
Testing effectiveness (Phase 2)Active Not RecruitingNCT06185764What this trial is testingVX-670 in Adult Participants With Myotonic Dystrophy 1 (DM1)Who this might be right forMyotonic Dystrophy Type 1 (DM1) Vertex Pharmaceuticals Incorporated 47
Not applicableStudy completedNCT03589612What this trial is testingRegression of Hamstring Flexibility and Performance in Children With Duchenne Muscular DystrophyWho this might be right forDuchenne Muscular DystrophyPerformanceFlexibility Hacettepe University 60
Early research (Phase 1)WithdrawnNCT02245711What this trial is testingCell Therapy in Limb Girdle Muscular DystrophyWho this might be right forLimb Girdle Muscular Dystrophy Neurogen Brain and Spine Institute
Not applicableLooking for participantsNCT05644522What this trial is testingNomad P-KAFO StudyWho this might be right forCerebrovascular AccidentPost-polio SyndromeSpinal Cord Injuries+3 more Shirley Ryan AbilityLab 36
Large-scale testing (Phase 3)Ended earlyNCT02814019What this trial is testingA Phase III Double-blind Study With Idebenone in Patients With Duchenne Muscular Dystrophy (DMD) Taking Glucocorticoid SteroidsWho this might be right forDuchenne Muscular Dystrophy (DMD) Santhera Pharmaceuticals 255
Not applicableLooking for participantsNCT03981575What this trial is testingEstab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)Who this might be right forMyotonic Dystrophy 1DM1 Virginia Commonwealth University 700
Early research (Phase 1)Study completedNCT05492734What this trial is testingAssess the Feasibility of Non-invasive Dried Blood SamplingWho this might be right forMuscular Dystrophies Edgewise Therapeutics, Inc. 10
Not applicableStudy completedNCT04907162What this trial is testingMusculoskeletal Nociceptive Pain in Participants With Neuromuscular DisordersWho this might be right forPompe Disease (Late-onset)Myotonic Dystrophy Type 1 (DM1)Myotonic Dystrophy Type 2+4 more LMU Klinikum 82
Testing effectiveness (Phase 2)Ended earlyNCT01826474What this trial is testingPhase IIb Study of PRO045 in Subjects With Duchenne Muscular DystrophyWho this might be right forDuchenne Muscular Dystrophy BioMarin Pharmaceutical 15
Testing effectiveness (Phase 2)Study completedNCT01976091What this trial is testingA Gene Transfer Therapy Study to Evaluate the Safety of SRP-9004 (Patidistrogene Bexoparvovec) in Participants With Limb-Girdle Muscular Dystrophy, Type 2D (LGMD2D)Who this might be right forLimb-Girdle Muscular Dystrophy, Type 2D Sarepta Therapeutics, Inc. 6
Not applicableEnrolling By InvitationNCT02413450What this trial is testingDerivation of Human Induced Pluripotent Stem (iPS) Cells to Heritable Cardiac ArrhythmiasWho this might be right forInherited Cardiac ArrythmiasLong QT Syndrome (LQTS)Brugada Syndrome (BrS)+7 more Johns Hopkins University 100
Not applicableActive Not RecruitingNCT02972580What this trial is testingCharacterization of Clinical Skeletal and Cardiac Impairment in Carriers of DMD and BMDWho this might be right forDuchenne Muscular DystrophyBecker Muscular Dystrophy Nationwide Children's Hospital 250