Large-scale testing (Phase 3)Active Not RecruitingNCT05329649
What this trial is testing
Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Severe Sickle Cell Disease (SCD)
Who this might be right for
Sickle Cell DiseaseHydroxyurea FailureHydroxyurea Intolerance+2 more
Vertex Pharmaceuticals Incorporated 13