Early research (Phase 1)Looking for participantsNCT05241444What this trial is testingCD4^LVFOXP3 in Participants With IPEXWho this might be right forIPEX Bacchetta, Rosa, MD 30
Not applicableLooking for participantsNCT04528355What this trial is testingData Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RICWho this might be right forPrimary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+2 more Paul Szabolcs 50
Testing effectiveness (Phase 2)Study completedNCT00919503What this trial is testingTreosulfan and Fludarabine Phosphate Before Donor Stem Cell Transplant in Treating Patients With Nonmalignant Inherited DisordersWho this might be right forNon-Neoplastic Hematologic and Lymphocytic Disorder Fred Hutchinson Cancer Center 98
Testing effectiveness (Phase 2)Looking for participantsNCT01962415What this trial is testingReduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCTWho this might be right forPrimary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+4 more Paul Szabolcs 100
Testing effectiveness (Phase 2)Not Yet RecruitingNCT07284641What this trial is testingHematopoietic Stem Cell Transplantation (HSCT) for Common Variable Immunodeficiency (CVID) and Other Autoimmune Manifestations of Primary Immune Regulatory Disorders (PIRD)Who this might be right forCommon Variable Immunodeficiency (CVID)Primary Immune Regulatory DisorderImmune Dysregulation+12 more Paul Szabolcs 25
Very early researchLooking for participantsNCT02356653What this trial is testingExpanded Access Protocol Using CD3+/CD19+ Depleted PBSCWho this might be right forLeukemiaInborn Errors of MetabolismBone Marrow Failure Syndromes+2 more Children's Hospital of Philadelphia 100