Not applicableStudy completedNCT01034969What this trial is testingFirazyr® Patient Registry (Icatibant Outcome Survey - IOS)Who this might be right forHereditary Angioedema (HAE) Shire 1,761
Testing effectiveness (Phase 2)UnknownNCT04371939What this trial is testingEfficacy and Safety of Romiplostim Versus Eltrombopag in the Treatment of Thrombocytopenia in Patients With Wiskott-Aldrich SyndromeWho this might be right forWiskott-Aldrich Syndrome Federal Research Institute of Pediatric Hematology, Oncology and Immunology 30
Not applicableStudy completedNCT05578417What this trial is testingReview the Treatment and Outcomes of Teenagers and Adults With Non-histaminergic Angioedema With Normal C1 Inhibitor in CanadaWho this might be right forHereditary Angioedema (HAE)Angioedema Takeda 60
Testing effectiveness (Phase 2)Looking for participantsNCT04414046What this trial is testingTCR Alpha Beta T-cell Depleted Haploidentical HCT in the Treatment of Primary Immunodeficiency and Inherited Metabolic Disorders in ChildrenWho this might be right forPrimary Immune Deficiency DisordersMetabolic Disease Johns Hopkins All Children's Hospital 17
Not applicableActive Not RecruitingNCT05469789What this trial is testingLanadelumab in Teenagers and Adults With Hereditary Angioedema (HAE)Who this might be right forHereditary Angioedema (HAE) Takeda 50
Early research (Phase 1)Study completedNCT04349800What this trial is testingA Single Dose Safety, Tolerability, Pharmacokinetic and Food Effect Study of KVD900 (Sebetralstat) in Healthy VolunteersWho this might be right forHereditary Angioedema KalVista Pharmaceuticals, Ltd. 84
Early research (Phase 1)Study completedNCT01923207What this trial is testingA Single Increasing Dose Study to Assess Safety and Tolerability of DX-2930 in Healthy SubjectsWho this might be right forHereditary Angioedema (HAE) Shire 32
Large-scale testing (Phase 3)Study completedNCT04654351What this trial is testingIcatibant (TAK-667) in Japanese Children and Teenagers With Acute Attacks of Hereditary AngioedemaWho this might be right forHereditary Angioedema Takeda 2
Testing effectiveness (Phase 2)Ended earlyNCT00968864What this trial is testingT-cell Depleted Alternative Donor TransplantationWho this might be right forAcute Lymphoblastic LeukemiaAcute Myeloid LeukemiaChronic Myeloid Leukemia+6 more Wake Forest University Health Sciences 53
Not applicableNot Yet RecruitingNCT06649643What this trial is testingInbon Errors of Immunity Attending Assiut University Children&Amp;#39;s Hospital: a Single Center StudyWho this might be right forPrimary Immunodeficiency Diseases (PID) Assiut University 60
Testing effectiveness (Phase 2)Study completedNCT05695248What this trial is testingNavenibart (STAR-0215) in Participants With Hereditary AngioedemaWho this might be right forHereditary Angioedema Astria Therapeutics, Inc. 29
Testing effectiveness (Phase 2)Study completedNCT00152893What this trial is testingTo Determine if Chromium Nicotinate Supplementation Will Improve Insulin Resistance in HIV Patients With Metabolic AbnormalitiesWho this might be right forHIV Infections Johane Allard 52
Testing effectiveness (Phase 2)Study completedNCT01410825What this trial is testingPilot and Feasibility Study of Hematopoietic Stem Cell Gene Transfer for the Wiskott-Aldrich SyndromeWho this might be right forWiskott-Aldrich Syndrome David Williams 5
Not applicableLooking for participantsNCT06169150What this trial is testingDetection and Characterization of Neurologic Manifestations of Inborn and Acquired Errors of ImmunityWho this might be right forNervous System DiseaseImmune System Disease National Institute of Allergy and Infectious Diseases (NIAID) 350
Not applicableStudy completedNCT02285348What this trial is testingOxidative Stress, Low Grade Inflammation, Tissue Breakdown and Biomarkers in Cerebrospinal Fluid of A-TWho this might be right forAtaxia Telangiectasia Johann Wolfgang Goethe University Hospital 18
Testing effectiveness (Phase 2)Study completedNCT00578643What this trial is testingMatched Unrelated or Non-Genotype Identical Related Donor Transplantation For Chronic Granulomatous DiseaseWho this might be right forChronic Granulomatous Disease Baylor College of Medicine 15
Not applicableStudy completedNCT02176239What this trial is testingMonitoring of 5% Treatment Naïve Intravenous Immunoglobulin (IVIg) Primary Immunodeficiency Disease (PIDD) Patients Using the CareExchange® System: A Pilot Study Using 5% Gammaplex® IVIg in the Home SettingWho this might be right forPrimary Immunodeficiency Disease (PIDD) BriovaRx Infusion Services 20
Not applicableStudy completedNCT02244450What this trial is testingGeneralized Neonatal Screening of Severe Combined ImmunodeficienciesWho this might be right forSevere Combined Immunodeficiency, Atypical Nantes University Hospital 190,539
Early research (Phase 1)Study completedNCT00001476What this trial is testingGene Therapy for Chronic Granulomatous Diseases - Long-term Follow-upWho this might be right forChronic Granulomatous DiseaseCommunicable Disease National Institute of Allergy and Infectious Diseases (NIAID) 14
Testing effectiveness (Phase 2)Not Yet RecruitingNCT03217617What this trial is testingSCID-X1 Gene Therapy Via Intravenous Lentiviral (Ivlv-X1) InjectionWho this might be right forSCID, X-Linked Shenzhen Geno-Immune Medical Institute 10