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Results for “Inherited Bone Marrow Failure Syndrome”

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Showing 20 of 0 results

Not applicableNot Yet RecruitingNCT07005297
What this trial is testing

Clinical Genetics Branch Eligibility Screening Survey

Who this might be right for
MelanomaLi-Fraumeni SyndromePulmonary Blastoma+7 more
National Cancer Institute (NCI) 1,000
Testing effectiveness (Phase 2)Study completedNCT00005898
What this trial is testing

Phase I/II Study of Total Body Irradiation, Cyclophosphamide, and Fludarabine Followed by Alternate Donor Hematopoietic Cell Transplantation in Patients With Fanconi's Anemia

Who this might be right for
Fanconi's Anemia
University of Minnesota 30
Early research (Phase 1)Study completedNCT00243399
What this trial is testing

Oxandrolone for the Treatment of Bone Marrow Aplasia in Fanconi Anemia

Who this might be right for
Fanconi Anemia
Children's Hospital Medical Center, Cincinnati 10
Not applicableWithdrawnNCT04331483
What this trial is testing

Assess a Physical Activity Program in Children, Adolescents and Young Adults Requiring Hematopoietic Stem Cell Allografts

Who this might be right for
Haematological MalignancyAcute LeukemiaMyelodysplastic Syndromes+3 more
Centre Leon Berard
Testing effectiveness (Phase 2)Study completedNCT02797977
What this trial is testing

A Phase 1/2 Trial SRA737 in Combination With Gemcitabine and Cisplatin or Gemcitabine Alone in Advanced Cancer Subjects

Who this might be right for
Advanced Solid Tumors
Sierra Oncology LLC - a GSK company 153
Early research (Phase 1)Study completedNCT00001399
What this trial is testing

Gene Therapy for the Treatment of Fanconi's Anemia Type C

Who this might be right for
Fanconi's AnemiaPancytopenia
National Heart, Lung, and Blood Institute (NHLBI) 9
Testing effectiveness (Phase 2)Study completedNCT00301834
What this trial is testing

Alemtuzumab, Fludarabine, and Busulfan Followed By Donor Stem Cell Transplant in Treating Young Patients With Hematologic Disorders

Who this might be right for
Congenital Amegakaryocytic ThrombocytopeniaDiamond-blackfan AnemiaLeukemia+2 more
University of California, San Francisco 35
Not applicableLooking for participantsNCT07145411
What this trial is testing

HPC Offered for PRESERVE Expansion

Who this might be right for
Bone Marrow Transplant (BMT)
Ossium Health, Inc. 10
Not applicableLooking for participantsNCT07186179
What this trial is testing

Mobilization of CD34+ Peripheral Blood Stem Cells in Patients With Diamond Blackfan Anemia Syndrome (DBAS)

Who this might be right for
Diamond Blackfan Anemia
Northwell Health 10
Very early researchStudy completedNCT00965666
What this trial is testing

Pilot Study of Etanercept (Enbrel) in Children With Fanconi Anemia

Who this might be right for
Fanconi Anemia
Children's Hospital Medical Center, Cincinnati 3
Not applicableLooking for participantsNCT06744283
What this trial is testing

Experience and Management of Cancer Screening-Related Anxiety in Fanconi Anemia

Who this might be right for
Fanconi Anemia
National Cancer Institute (NCI) 20
Testing effectiveness (Phase 2)Ended earlyNCT00968864
What this trial is testing

T-cell Depleted Alternative Donor Transplantation

Who this might be right for
Acute Lymphoblastic LeukemiaAcute Myeloid LeukemiaChronic Myeloid Leukemia+6 more
Wake Forest University Health Sciences 53
Testing effectiveness (Phase 2)Study completedNCT00305708
What this trial is testing

Busulfan, Antithymocyte Globulin, and Fludarabine Followed By a Donor Stem Cell Transplant in Treating Young Patients With Blood Disorders, Bone Marrow Disorders, Chronic Myelogenous Leukemia in First Chronic Phase, or Acute Myeloid Leukemia in First Remission

Who this might be right for
Congenital Amegakaryocytic ThrombocytopeniaDiamond-blackfan AnemiaFanconi Anemia+3 more
University of California, San Francisco 40
Not applicableStudy completedNCT00856388
What this trial is testing

Fludarabine Phosphate, Melphalan, Total-Body Irradiation, Donor Stem Cell Transplant in Treating Patients With Hematologic Cancer or Bone Marrow Failure Disorders

Who this might be right for
Accelerated Phase Chronic Myelogenous LeukemiaAcute Myeloid Leukemia With Multilineage Dysplasia Following Myelodysplastic SyndromeAdult Acute Lymphoblastic Leukemia in Remission+97 more
Roswell Park Cancer Institute 62
Not applicableStudy completedNCT06958380
What this trial is testing

Corrective Exercise and Rehabilitation in Fanconi Anemia: A Case Study

Who this might be right for
Fanconi Anemia
Pardis Specialized Wellness Institute 1
Not applicableStudy completedNCT00244010
What this trial is testing

Partially Matched Stem Cell Transplantation for Patients With Refractory Severe Aplastic Anemia or Refractory Cytopenias

Who this might be right for
Anemia, AplasticAmegakaryocytic ThrombocytopeniaDiamond-Blackfan Anemia+1 more
St. Jude Children's Research Hospital 4
Testing effectiveness (Phase 2)Looking for participantsNCT02143830
What this trial is testing

HSCT for Patients With Fanconi Anemia Using Risk-Adjusted Chemotherapy

Who this might be right for
Fanconi AnemiaSevere Marrow FailureMyelodysplastic Syndrome (MDS)+1 more
Children's Hospital Medical Center, Cincinnati 70
Testing effectiveness (Phase 2)Active Not RecruitingNCT03206086
What this trial is testing

Eltrombopag for Fanconi Anemia

Who this might be right for
Fanconi Anemia
National Heart, Lung, and Blood Institute (NHLBI) 25
Not applicableStudy completedNCT03609827
What this trial is testing

Study of Melphalan Drug Exposure in Pediatric Hematopoietic Stem Cell Transplant Patients

Who this might be right for
Hematologic MalignanciesNonmalignant DiseasesImmunodeficiencies+5 more
University of California, San Francisco 25
Testing effectiveness (Phase 2)Ended earlyNCT00167206
What this trial is testing

Stem Cell Transplantation for Fanconi Anemia

Who this might be right for
Fanconi Anemia
Masonic Cancer Center, University of Minnesota 16
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