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Results for “Inherited Bone Marrow Failure Syndromes”

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Showing 20 of 0 results

Testing effectiveness (Phase 2)Ended earlyNCT00617929
What this trial is testing

Antithymocyte Globulin, Clofarabine, and Rituximab in Treating Patients After an Unsuccessful Stem Cell Transplant

Who this might be right for
Cancer
Masonic Cancer Center, University of Minnesota 12
Testing effectiveness (Phase 2)Study completedNCT00061763
What this trial is testing

Study of Deferasirox in Iron Overload From Beta-thalassemia Unable to be Treated With Deferoxamine or Chronic Anemias

Who this might be right for
Beta-thalassemiaMyelodysplastic SyndromesFanconi Syndrome+2 more
Novartis Pharmaceuticals 175
Not applicableEnded earlyNCT05910853
What this trial is testing

Whole Blood Biospecimen Collection for Subjects With Fanconi Anemia

Who this might be right for
Fanconi Anemia
Sanguine Biosciences 4
Testing effectiveness (Phase 2)Study completedNCT01044186
What this trial is testing

A Protocol to Allow Treatment With ICL670 for Patients With or at Risk of Life-threatening Complications of Transfusional Iron Overload Who Are Unable to Tolerate Other Iron Chelators Because of Documented Severe Toxicity

Who this might be right for
Transfusional Iron Overload
Novartis Pharmaceuticals 30
Testing effectiveness (Phase 2)Study completedNCT01529827
What this trial is testing

Fludarabine Phosphate, Melphalan, and Low-Dose Total-Body Irradiation Followed by Donor Peripheral Blood Stem Cell Transplant in Treating Patients With Hematologic Malignancies

Who this might be right for
Accelerated Phase Chronic Myelogenous LeukemiaAdult Acute Lymphoblastic Leukemia in RemissionAdult Acute Myeloid Leukemia in Remission+75 more
Roswell Park Cancer Institute 94
Testing effectiveness (Phase 2)Looking for participantsNCT04356469
What this trial is testing

TCR Alpha Beta T-cell Depleted Haploidentical HCT in the Treatment of Non-Malignant Hematological Disorders in Children

Who this might be right for
Hemoglobinopathy (Disorder)Severe Aplastic AnemiaBone Marrow Failure Syndrome
Johns Hopkins All Children's Hospital 17
Not applicableStudy completedNCT03576742
What this trial is testing

Severe Immune Cytopenia Registry Www.Sic-reg.Org

Who this might be right for
Immune ThrombocytopeniaAutoimmune Hemolytic AnemiaEvans Syndrome+1 more
Medical University of Graz 80
Early research (Phase 1)Study completedNCT00569283
What this trial is testing

Donor Natural Killer Cell Infusion in Preventing Relapse or Graft Failure in Patients Who Have Undergone Donor Bone Marrow Transplant

Who this might be right for
Cancer
Asan Medical Center 18
Testing effectiveness (Phase 2)Study completedNCT00004143
What this trial is testing

Allogeneic Mixed Chimerism Stem Cell Transplant Using Campath for Hemoglobinopathies & Bone Marrow Failure Syndromes

Who this might be right for
Sickle Cell AnemiaSevere Aplastic AnemiaParoxysmal Nocturnal Hemoglobinuria (PNH)+1 more
David Rizzieri, MD 2
Not applicableLooking for participantsNCT05436587
What this trial is testing

Mutations and Phenotypes of Unclassifiable Inherited Bone Marrow Failure Syndromes

Who this might be right for
Inherited BMF Syndrome
Sohag University 250
Testing effectiveness (Phase 2)Study completedNCT03157804
What this trial is testing

Lentiviral-mediated Gene Therapy of Fanconi Anemia Patients Subtype A

Who this might be right for
Fanconi Anemia
Hospital Infantil Universitario Niño Jesús, Madrid, Spain 9
Early research (Phase 1)Study completedNCT00692926
What this trial is testing

Unrelated Umbilical Cord Blood Transplantation Augmented With ALDHbr Umbilical Cord Blood Cells

Who this might be right for
MDSAnemia, AplasticInborn Errors of Metabolism+2 more
Joanne Kurtzberg, MD 37
Not applicableStudy completedNCT05598515
What this trial is testing

Time-restricted Feeding to Reduce Inflammation in Fanconi Anemia

Who this might be right for
Fanconi Anemia
Children's Hospital Medical Center, Cincinnati 3
Testing effectiveness (Phase 2)Study completedNCT00258427
What this trial is testing

Hematopoietic Stem Cell Transplantation in High Risk Patients With Fanconi Anemia

Who this might be right for
Fanconi Anemia
Masonic Cancer Center, University of Minnesota 14
Testing effectiveness (Phase 2)Active Not RecruitingNCT05796570
What this trial is testing

A Pilot Study to Evaluate the Feasibility of Post-Hematopoietic Stem Cell Transplant Prophylaxis With Decitabine Combined With Filgrastim for Children and Young Adults With AML, MDS and Related Myeloid Malignancies

Who this might be right for
Acute Myeloid LeukemiaMyelodysplastic SyndromesMyeloid Malignancies+4 more
Franziska Wachter 29
Testing effectiveness (Phase 2)Not Yet RecruitingNCT07660783
What this trial is testing

Naive T Cell Deplete Grafts for GVHD Prevention in Non-Malignant Diseases

Who this might be right for
Bone Marrow FailureHemoglobinopathiesPrimary Immune Deficiency (PID)+4 more
Fred Hutchinson Cancer Center 40
Not applicableLooking for participantsNCT00027274
What this trial is testing

Cancer in Inherited Bone Marrow Failure Syndromes

Who this might be right for
Diamond Blackfan AnemiaDyskeratosis CongenitaFanconi Anemia+2 more
National Cancer Institute (NCI) 4,000
Testing effectiveness (Phase 2)Study completedNCT00003662
What this trial is testing

Umbilical Cord Blood Transplantation in Treating Patients With Hematologic Cancer or Other Hematologic or Metabolic Diseases

Who this might be right for
Graft Versus Host DiseaseLeukemiaMyelodysplastic Syndromes+1 more
Roswell Park Cancer Institute 90
Early research (Phase 1)Study completedNCT00272857
What this trial is testing

Bone Marrow Cell Gene Transfer in Individuals With Fanconi Anemia

Who this might be right for
Fanconi Anemia
Boston Children's Hospital 3
Testing effectiveness (Phase 2)Ended earlyNCT03333486
What this trial is testing

Fludarabine Phosphate, Cyclophosphamide, Total Body Irradiation, and Donor Stem Cell Transplant in Treating Patients With Blood Cancer

Who this might be right for
Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 PositiveAcute Leukemia in RemissionAcute Lymphoblastic Leukemia+34 more
Roswell Park Cancer Institute 31
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