Not applicableNot Yet RecruitingNCT07500493What this trial is testingTele-Rehabilitation in Adults With Cystic FibrosisWho this might be right forCystic FibrosisSarcopeniaFrailty King Saud University 76
Large-scale testing (Phase 3)Study completedNCT03920540What this trial is testingGC1111 in Hunter Syndrom PatientsWho this might be right forHunter Syndrome Green Cross Corporation 32
Testing effectiveness (Phase 2)Ended earlyNCT03080480What this trial is testingPioglitazone Therapy for Chronic Granulomatous DiseaseWho this might be right forChronic Granulomatous Disease Children's Hospital of Fudan University 3
Not applicableStudy completedNCT00007046What this trial is testingGenetic Study of Patients and Families With Diaphyseal Medullary Stenosis With Malignant Fibrous Histiocytoma of the BoneWho this might be right forStenosisHistiocytoma National Center for Research Resources (NCRR)
Testing effectiveness (Phase 2)Active Not RecruitingNCT05755997What this trial is testingCERebrolysin In CADASILWho this might be right forCadasil Ever Neuro Pharma GmbH 30
Not applicableUnknownNCT02058342What this trial is testingFamily-based Intervention for Youth With Prader-Willi Syndrome: The Active Play at Home StudyWho this might be right forPrader Willi SyndromeChildhood Obesity California State University, Fullerton 115
Not applicableStudy completedNCT01327924What this trial is testingUsability and Tolerability of the Norditropin NordiFlex® Injection Device in Children Never Previously Treated With Growth HormoneWho this might be right forGrowth Hormone DisorderGrowth Hormone Deficiency in ChildrenGenetic Disorder+6 more Novo Nordisk A/S 77
Testing effectiveness (Phase 2)Study completedNCT00004359What this trial is testingPhase II Pilot Study of Extracorporeal Phototherapy for Epidermolysis Bullosa AcquisitaWho this might be right forEpidermolysis Bullosa Acquisita National Center for Research Resources (NCRR) 10
Not applicableUnknownNCT03123003What this trial is testingBone Age Assessment in Children Using Ultrasound Compared to Wrist X-rayWho this might be right forShort StatureGrowth Disorders Meir Medical Center 300
Testing effectiveness (Phase 2)Looking for participantsNCT06898450What this trial is testingAssess the Safety, Tolerability, and Efficacy of NDI-219216 in Patients With Advanced Solid Tumors.Who this might be right forAdvanced Solid Tumors CancerMSI-H Cancer Nimbus Wadjet, Inc. 134
Testing effectiveness (Phase 2)WithdrawnNCT05146882What this trial is testingAn Extension Study of Belcesiran in Patients With Alpha-1 Antitrypsin Deficiency Associated Liver Disease (AATLD)Who this might be right forAlpha 1-Antitrypsin Deficiency Dicerna Pharmaceuticals, Inc., a Novo Nordisk company
Not applicableStudy completedNCT00004361What this trial is testingStudy of the Relationship Between Calcium Levels and Intact Parathyroid Hormone (iPTH) in Adults With Repaired or Palliated Conotruncal Cardiac DefectsWho this might be right forHypoparathyroidismTetralogy of FallotPulmonary Valve Stenosis+3 more National Center for Research Resources (NCRR) 150
Not applicableStudy completedNCT02199717What this trial is testingAn Institutional Pilot Study to Investigate Physical Activity Patterns in Boys With HemophiliaWho this might be right forHemophilia AHemophilia BFactor VIII Deficiency+1 more The Hospital for Sick Children 66
Not applicableStudy completedNCT04153110What this trial is testingCerebello-Spinal tDCS as Rehabilitative Intervention in Neurodegenerative AtaxiaWho this might be right forAtaxiaSpinocerebellar AtaxiasSpinocerebellar Ataxia Type 1+5 more Azienda Socio Sanitaria Territoriale degli Spedali Civili di Brescia 61
Early research (Phase 1)Study completedNCT03899246What this trial is testingSickle Cell Pain: Intervention With Capsaicin ExposureWho this might be right forNeuropathic PainSickle Cell Disease Children's Hospital of Michigan 10
Not applicableUnknownNCT06539169What this trial is testingFLOWER: Following Longitudinal Outcomes With Epidemiology for Rare DiseasesWho this might be right forAlpha-ThalassemiaBeta-ThalassemiaAmyloidosis+14 more xCures 1,000
Not applicableAvailableNCT03778424What this trial is testingAn Extended Access Program (EAP) for Participants Who Have Completed Rufinamide Study E2080-G000-303Who this might be right forLennox Gastaut Syndrome Eisai Inc.
Large-scale testing (Phase 3)Study completedNCT02950883What this trial is testingSaline Hypertonic in Preschoolers + CTWho this might be right forCystic Fibrosis University of Washington, the Collaborative Health Studies Coordinating Center 116
Not applicableUnknownNCT05635266What this trial is testingTissue Repository Providing Annotated Biospecimens for Approved Investigator-directed Biomedical Research InitiativesWho this might be right forAge-Related Macular DegenerationAllergiesAlpha-Gal Syndrome+44 more Sanguine Biosciences 20,000
Post-approval studies (Phase 4)Study completedNCT01018056What this trial is testingDeveloping New Treatments for Tourette Syndrome: Therapeutic Trials With Modulators of Glutamatergic NeurotransmissionWho this might be right forTourette Syndrome Johns Hopkins University 39