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Results for “Inherited Retinal Dystrophy Associated With RPE65 Mutations”

6 trials

Showing 6 of 6 results

Early research (Phase 1)Active Not RecruitingNCT06196827
What this trial is testing

Safety and Tolerability of LX101 for Inherited Retinal Dystrophy Associated With RPE65 Mutations

Who this might be right for
Inherited Retinal Dystrophy Associated With RPE65 Mutations
Innostellar Biotherapeutics Co.,Ltd 9
Not applicableStudy completedNCT03597399
What this trial is testing

A Patient Registry Study for Patients Treated With Voretigene Neparvovec in US

Who this might be right for
Confirmed Biallelic RPE65 Mutation-associated Retinal Dystrophy
Spark Therapeutics, Inc. 87
Large-scale testing (Phase 3)Active Not RecruitingNCT00999609
What this trial is testing

Safety and Efficacy Study in Subjects With Leber Congenital Amaurosis

Who this might be right for
Inherited Retinal Dystrophy Due to RPE65 MutationsLeber Congenital Amaurosis
Spark Therapeutics, Inc. 31
Large-scale testing (Phase 3)Active Not RecruitingNCT07054632
What this trial is testing

Efficacy and Safety of LX101 for Inherited Retinal Dystrophy Associated With RPE65 Mutations

Who this might be right for
Inherited Retinal Dystrophy Associated With RPE65 Mutations
Innostellar Biotherapeutics Co.,Ltd 30
Not applicableActive Not RecruitingNCT03602820
What this trial is testing

Long-term Follow-up Study in Subjects Who Received Voretigene Neparvovec-rzyl (AAV2-hRPE65v2)

Who this might be right for
Inherited Retinal Dystrophy Due to RPE65 Mutations
Genentech, Inc. 41
Testing effectiveness (Phase 2)Active Not RecruitingNCT06212297
What this trial is testing

Fellow-eye Study (FE) of LX101 in Subjects With Inherited Retinal Dystrophy

Who this might be right for
Inherited Retinal Dystrophy
Innostellar Biotherapeutics Co.,Ltd 9

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