Early research (Phase 1)Ended earlyNCT05906251
What this trial is testing
A Gene Transfer Study to Evaluate the Safety, Tolerability and Efficacy of SRP-6004 in Ambulatory Participants With Limb Girdle Muscular Dystrophy, Type 2B/R2 (LGMD2B/R2, Dysferlin [DYSF] Related)
Who this might be right for
Limb Girdle Muscular Dystrophy
Sarepta Therapeutics, Inc. 2