Not applicableWithdrawnNCT04007562
What this trial is testing
Acute Rhabdomyolysis and Muscle Pain Associated With Mutations in the LPIN1 Gene - A Retrospective Study Describing the Safety and Efficacy of Hydroxychloroquine Sulfate Given on a Compassionate Basis to Patients Suffering From Lipin-1 Deficiency
Who this might be right for
LIPIN1 Deficiency
Assistance Publique - Hôpitaux de Paris