Not applicableStudy completedNCT05431127What this trial is testingHigh Dose Inspiratory Muscle Training in LOPDWho this might be right forLate-Onset Pompe DiseaseLysosomal Disease Duke University 34
Testing effectiveness (Phase 2)Looking for participantsNCT07123155What this trial is testingStudy of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)Who this might be right forPompe Disease Shionogi 45
Large-scale testing (Phase 3)Active Not RecruitingNCT03911505What this trial is testingZIP Study-OL Study of Safety, PK, Efficacy, PD, Immunogenicity of ATB200/AT2221 in Pediatrics Aged 0 to < 18 y.o. w/LOPDWho this might be right forPompe Disease (Late-onset) Amicus Therapeutics 21
Not applicableEnded earlyNCT02191917What this trial is testingRespiratory Muscle Strength in Patients With Late-onset Pompe Disease (LOPD)Who this might be right forLate-onset Pompe Disease BioMarin Pharmaceutical 8
Early research (Phase 1)Looking for participantsNCT07354724What this trial is testingEvaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe DiseaseWho this might be right forLate-onset Pompe Disease Denali Therapeutics Inc. 32
Not applicableStudy completedNCT03893240What this trial is testingNeutralizing Antibody Seroprevalence Study With a Retrospective Component in Participants With Late-Onset Pompe DiseaseWho this might be right forPompe DiseasePompe Disease (Late-onset)Glycogen Storage Disease Type 2+3 more Spark Therapeutics, Inc. 61
Large-scale testing (Phase 3)Study completedNCT04138277What this trial is testingAssess the Long-term Safety and Efficacy of ATB200/AT2221 in Adult Subjects With Late-Onset Pompe Disease (LOPD)Who this might be right forPompe Disease (Late-onset) Amicus Therapeutics 119
Early research (Phase 1)Study completedNCT01859624What this trial is testingAlbuterol in Individuals With Late Onset Pompe Disease (LOPD)Who this might be right forPompe Disease Duke University 8
Not applicableUnknownNCT05951790What this trial is testingInspiratory Muscle Training (IMT) in Adult People With Pompe DiseaseWho this might be right forGlycogen Storage Disease Type IIPompe Disease (Late-onset) Fondazione Don Carlo Gnocchi Onlus 20
Very early researchNot Yet RecruitingNCT06178432What this trial is testingEvaluation of the Safety, Tolerability and Efficacy of Gene Therapy Drug for Late Onset Pompe Disease (LOPD)Who this might be right forPompe Disease (Late-onset) Huashan Hospital 6
Not applicableStudy completedNCT02765828What this trial is testingIdentification of Tongue Involvement in Late-Onset Pompe DiseaseWho this might be right forMyopathyNeuropathyGlycogen Storage Disease Type II (Late-onset Pompe Disease) Duke University 73
Not applicableLooking for participantsNCT05989620What this trial is testingLong-Term Development of Muscular Dystrophy Outcome AssessmentsWho this might be right forLGMD1BLGMD1CLGMD1D+26 more Virginia Commonwealth University 1,000
Testing effectiveness (Phase 2)WithdrawnNCT04094948What this trial is testingPhase II Clinical Trial of Clenbuterol in Adult Patients With Pompe DiseaseWho this might be right forPompe Disease (Late-onset) Duke University
Early research (Phase 1)Study completedNCT02240407What this trial is testingRe-administration of Intramuscular AAV9 in Patients With Late-Onset Pompe DiseaseWho this might be right forPompe Disease University of Florida 2
Not applicableStudy completedNCT02801539What this trial is testingRespiratory Muscle Training in L-Onset Pompe Disease (LOPD)Who this might be right forGlycogen Storage Disease Type II Duke University 22
Testing effectiveness (Phase 2)Active Not RecruitingNCT04093349What this trial is testingA Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE)Who this might be right forPompe DiseasePompe Disease (Late-onset)Glycogen Storage Disease Type 2+4 more Spark Therapeutics, Inc. 4
Not applicableUnknownNCT05272969What this trial is testingPompe & Pain - Study to Assess Nociceptive Pain in Adult Patients With Pompe DiseaseWho this might be right forPompe Disease (Late-onset)Inclusion Body MyositisSpinal Muscular Atrophy Type 3+1 more LMU Klinikum 95
Not applicableStudy completedNCT03255213What this trial is testingLingual Muscle Training in Late-Onset Pompe Disease (LOPD)Who this might be right forGlycogen Storage Disease Duke University 5
Testing effectiveness (Phase 2)Study completedNCT01885936What this trial is testingSafety and Efficacy of Albuterol in Individuals With Late-onset Pompe DiseaseWho this might be right forPompe Disease Duke University 16
Testing effectiveness (Phase 2)Active Not RecruitingNCT04174105What this trial is testingGene Transfer Study in Patients With Late Onset Pompe DiseaseWho this might be right forPompe Disease (Late-onset) Astellas Gene Therapies 11