Not applicableLooking for participantsNCT03333200What this trial is testingLongitudinal Study of Neurodegenerative DisordersWho this might be right forMLDKrabbe DiseaseALD+24 more University of Pittsburgh 1,500
Not applicableEnrolling By InvitationNCT03655223What this trial is testingEarly Check: Expanded Screening in NewbornsWho this might be right forSpinal Muscular AtrophyFragile X SyndromeFragile X - Premutation+182 more RTI International 30,000
Testing effectiveness (Phase 2)Looking for participantsNCT06078969What this trial is testingOral Prednisone in Treating LCH of Bone in Childhood and AdolescenceWho this might be right forLangerhans Cell Histiocytosis of Bone Shanghai Changzheng Hospital 118
Early research (Phase 1)Active Not RecruitingNCT00710892What this trial is testingCASPALLO: Allodepleted T Cells Transduced With Inducible Caspase 9 Suicide GeneWho this might be right forAcute Lymphoblastic LeukemiaNon-Hodgkin's LymphomaMyelodysplastic Syndrome+1 more Baylor College of Medicine 10
Testing effectiveness (Phase 2)Study completedNCT03220035What this trial is testingVemurafenib in Treating Patients With Relapsed or Refractory Advanced Solid Tumors, Non-Hodgkin Lymphoma, or Histiocytic Disorders With BRAF V600 Mutations (A Pediatric MATCH Treatment Trial)Who this might be right forAdvanced Malignant Solid NeoplasmAnn Arbor Stage III Childhood Non-Hodgkin LymphomaAnn Arbor Stage IV Childhood Non-Hodgkin Lymphoma+20 more National Cancer Institute (NCI) 4
Testing effectiveness (Phase 2)Study completedNCT01273766What this trial is testingDeferasirox in Treating Iron Overload Caused By Blood Transfusions in Patients With Hematologic MalignanciesWho this might be right forAcute Undifferentiated LeukemiaAdult Acute Lymphoblastic Leukemia in RemissionAdult Acute Myeloid Leukemia in Remission+133 more Wake Forest University Health Sciences 16
Early research (Phase 1)Study completedNCT01586455What this trial is testingHuman Placental-Derived Stem Cell TransplantationWho this might be right forMucopolysaccharidosis IMucopolysaccharidosis VIAdrenoleukodystrophy+13 more New York Medical College 43
Testing effectiveness (Phase 2)Study completedNCT00730314What this trial is testingUnrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood CellsWho this might be right forSickle Cell DiseaseThalassemiaAnemia+9 more Children's Hospital Los Angeles 25
Early research (Phase 1)Active Not RecruitingNCT01494103What this trial is testingAdministration of Donor T Cells With the Caspase-9 Suicide GeneWho this might be right forAcute Lymphoblastic LeukemiaMyelodysplastic SyndromeAcute Myeloid Leukemia+7 more Baylor College of Medicine 15
Testing effectiveness (Phase 2)Study completedNCT03096782What this trial is testingUmbilical Cord Blood Transplant With Added Sugar and Chemotherapy and Radiation Therapy in Treating Patients With Leukemia or LymphomaWho this might be right forAccelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 PositiveAcute Biphenotypic LeukemiaAcute Leukemia+19 more M.D. Anderson Cancer Center 6
Testing effectiveness (Phase 2)Looking for participantsNCT01962415What this trial is testingReduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCTWho this might be right forPrimary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+4 more Paul Szabolcs 100
Testing effectiveness (Phase 2)Study completedNCT03526250What this trial is testingPalbociclib in Treating Patients With Relapsed or Refractory Rb Positive Advanced Solid Tumors, Non-Hodgkin Lymphoma, or Histiocytic Disorders With Activating Alterations in Cell Cycle Genes (A Pediatric MATCH Treatment Trial)Who this might be right forAdvanced Malignant Solid NeoplasmRecurrent Childhood EpendymomaRecurrent Ewing Sarcoma+29 more National Cancer Institute (NCI) 23
Not applicableLooking for participantsNCT02402244What this trial is testingProject: Every Child for Younger Patients With CancerWho this might be right forAdrenal Gland PheochromocytomaCarcinoma In SituCentral Nervous System Neoplasm+15 more Children's Oncology Group 75,000
Testing effectiveness (Phase 2)Active Not RecruitingNCT04320888What this trial is testingSelpercatinib for the Treatment of Advanced Solid Tumors, Lymphomas, or Histiocytic Disorders With Activating RET Gene Alterations, a Pediatric MATCH Treatment TrialWho this might be right forHematopoietic and Lymphatic System NeoplasmRecurrent EpendymomaRecurrent Ewing Sarcoma+35 more National Cancer Institute (NCI) 1
Testing effectiveness (Phase 2)Study completedNCT00368355What this trial is testingT Cell Depletion for Recipients of HLA Haploidentical Related Donor Stem Cell GraftsWho this might be right forAcute Lymphoblastic LeukemiaNon Hodgkins LymphomaMyelodysplastic Syndrome+6 more Baylor College of Medicine 46
Not applicableLooking for participantsNCT04528355What this trial is testingData Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RICWho this might be right forPrimary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+2 more Paul Szabolcs 50
Not applicableUnknownNCT00005900What this trial is testingStudy of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell TransplantationWho this might be right forI Cell DiseaseFucosidosisGloboid Cell Leukodystrophy+9 more Fairview University Medical Center 10
Testing effectiveness (Phase 2)UnknownNCT00084695What this trial is testingUmbilical Cord Blood for Stem Cell Transplantation in Treating Young Patients With Malignant or Nonmalignant DiseasesWho this might be right forChildhood Langerhans Cell HistiocytosisFanconi AnemiaLeukemia+5 more Milton S. Hershey Medical Center 25
Large-scale testing (Phase 3)Study completedNCT00176904What this trial is testingStem Cell Transplant for Inborn Errors of MetabolismWho this might be right forAdrenoleukodystrophyMetachromatic LeukodystrophyGloboid Cell Leukodystrophy+8 more Masonic Cancer Center, University of Minnesota 135
Early research (Phase 1)Ended earlyNCT02231710What this trial is testingSafety Study of Gene Modified Donor T Cell Infusion After Stem Cell Transplant for Non-Malignant DiseasesWho this might be right forPrimary Immune Deficiency DisordersHemophagocytic LymphohistiocytosisInherited Bone Marrow Failure Syndrome+2 more Bellicum Pharmaceuticals 1