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Results for “Late Onset Pompe Disease”

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Showing 20 of 0 results

Testing effectiveness (Phase 2)Not Yet RecruitingNCT07750990
What this trial is testing

An Extension Study of S-606001 in Participants With Late-onset Pompe Disease (LOPD)

Who this might be right for
Pompe Disease
Shionogi 60
Post-approval studies (Phase 4)Not Yet RecruitingNCT06575829
What this trial is testing

Treatment Frequency Reduction in Pompe Disease

Who this might be right for
Pompe Disease (Late-onset)GAA DeficiencyGlycogen Storage Disease Type II+1 more
Erasmus Medical Center 10
Not applicableStudy completedNCT00731081
What this trial is testing

Study About the Evolution of Severe Late Onset Pompe Disease Patient With Pulmonary Dysfunction and Receiving Myozyme®

Who this might be right for
Pompe Disease (Late-Onset)Glycogen Storage Disease Type II (GSD II)Glycogenesis 2 Acid Maltase Deficiency
Genzyme, a Sanofi Company 8
Not applicableStudy completedNCT04120168
What this trial is testing

Study Determining the Frequency of Duchenne Muscular Dystrophy and Late-onset Pompe Disease

Who this might be right for
Duchenne Muscular DystrophyPompe Disease (Late-onset)
Turkish Society of Pediatric Gastroenterology, Hepatology and Nutrition 590
Not applicableStudy completedNCT03255213
What this trial is testing

Lingual Muscle Training in Late-Onset Pompe Disease (LOPD)

Who this might be right for
Glycogen Storage Disease
Duke University 5
Not applicableUnknownNCT04981210
What this trial is testing

High Risk Screen of Childhood Late-onset Pompe Disease in Pediatric Outpatient Clinics

Who this might be right for
Pompe Disease
National Taiwan University Hospital 1,500
Large-scale testing (Phase 3)Study completedNCT02782741
What this trial is testing

Study to Compare the Efficacy and Safety of Enzyme Replacement Therapies Avalglucosidase Alfa and Alglucosidase Alfa Administered Every Other Week in Patients With Late-onset Pompe Disease Who Have Not Been Previously Treated for Pompe Disease

Who this might be right for
Glycogen Storage Disease Type II;Pompe's Disease
Genzyme, a Sanofi Company 101
Testing effectiveness (Phase 2)Looking for participantsNCT07123155
What this trial is testing

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

Who this might be right for
Pompe Disease
Shionogi 45
Not applicableLooking for participantsNCT05989620
What this trial is testing

Long-Term Development of Muscular Dystrophy Outcome Assessments

Who this might be right for
LGMD1BLGMD1CLGMD1D+26 more
Virginia Commonwealth University 1,000
Not applicableStudy completedNCT02824068
What this trial is testing

Long-term Outcome in Late-onset Pompe Disease Treated Beyond 36 Months (STIG-Pompe-Study)

Who this might be right for
Pompe Disease
LMU Klinikum 112
Testing effectiveness (Phase 2)UnknownNCT06130228
What this trial is testing

Nutritional Therapy in Late-onset Pompe Disease

Who this might be right for
Pompe DiseaseMuscle LossObesity+5 more
McMaster University 28
Post-approval studies (Phase 4)Study completedNCT01288027
What this trial is testing

Exploratory Muscle Biopsy Assessment Study in Patients With Late-Onset Pompe Disease Treated With Alglucosidase Alfa

Who this might be right for
Pompe Disease (Late-Onset)Glycogen Storage Disease Type II (GSD II)Glycogenesis 2 Acid Maltase Deficiency
Genzyme, a Sanofi Company 16
Large-scale testing (Phase 3)Study completedNCT00158600
What this trial is testing

A Placebo-Controlled Study of Safety and Effectiveness of Myozyme (Alglucosidase Alfa) in Patients With Late-Onset Pompe Disease

Who this might be right for
Pompe Disease (Late-onset)Glycogen Storage Disease Type II (GSD-II)Acid Maltase Deficiency Disease+1 more
Genzyme, a Sanofi Company 90
Testing effectiveness (Phase 2)Looking for participantsNCT06391736
What this trial is testing

Evaluation of the Safety and Efficacy of Late-onset Pompe Disease Gene Therapy Drug

Who this might be right for
Pompe Disease (Late-onset)
GeneCradle Inc 33
Not applicableStudy completedNCT00566878
What this trial is testing

Pompe Lactation Sub-Registry

Who this might be right for
Glycogen Storage DiseasePompe Disease
Genzyme, a Sanofi Company 2
Not applicableUnknownNCT00713245
What this trial is testing

A Long Term Follow up Study in Late-onset Pompe Disease

Who this might be right for
Pompe Disease
National Taiwan University Hospital 70
Testing effectiveness (Phase 2)Study completedNCT01230801
What this trial is testing

Safety/Tolerability/Pharmacokinetic (PK)/Pharmacodynamics (PD) Study of BMN701 in Patients With Late-Onset Pompe Disease

Who this might be right for
Pompe Disease
BioMarin Pharmaceutical 22
Not applicableStudy completedNCT00113035
What this trial is testing

Screening Protocol to Evaluate Acid Alpha-Glucosidase (GAA) Activity and GAA Gene Mutations in Patients With Late Onset Pompe Disease

Who this might be right for
Pompe Disease
Genzyme, a Sanofi Company 60
Very early researchStudy completedNCT06109948
What this trial is testing

Study to Assess the Safety, Tolerability, PK and PD of ABX1100

Who this might be right for
HealthyLate Onset Pompe Disease
Aro Biotherapeutics 46
Testing effectiveness (Phase 2)Looking for participantsNCT07282847
What this trial is testing

Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)

Who this might be right for
Pompe Disease (Late-onset)Pompe Disease Late-OnsetLOPD
AskBio Inc 12
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