Testing effectiveness (Phase 2)Study completedNCT01886378
What this trial is testing
UX007 (Triheptanoin) in Participants With Long-Chain Fatty Acid Oxidation Disorders (LC-FAOD)
Who this might be right for
Long-chain Fatty Acid Oxidation Disorders (LC-FAOD)Carnitine Palmitoyltransferase (CPT II) DeficiencyVery Long Chain Acyl-CoA Dehydrogenase (VLCAD) Deficiency+2 more
Ultragenyx Pharmaceutical Inc 29