Not applicableStudy completedNCT03576729What this trial is testingMRS to Determine Neuroinflammation and Oxidative Stress in MPS IWho this might be right forMucopolysaccharidosis Type I University of Minnesota 30
Not applicableStudy completedNCT01873911What this trial is testingNeurobehavioral Phenotypes in MPS IIIWho this might be right forSanfilippo Syndrome Type ASanfilippo Syndrome Type BHurler Syndrome University of Minnesota 30
Early research (Phase 1)Study completedNCT01173016What this trial is testingAdministration of IV Laronidase Post Bone Marrow Transplant in HurlerWho this might be right forHurler Syndrome Masonic Cancer Center, University of Minnesota 11
Testing effectiveness (Phase 2)WithdrawnNCT04284254What this trial is testingMT2018-18: Sleeping Beauty Transposon-Engineered Plasmablasts for Hurler Syndrome Post Allo HSCTWho this might be right forMucopolysaccharidosis Type IH (MPS IH, Hurler Syndrome)Mucopolysaccharidosis Type IHMPS IH, Hurler Syndrome Masonic Cancer Center, University of Minnesota
Large-scale testing (Phase 3)Active Not RecruitingNCT06149403What this trial is testingInvestigate the Efficacy and Safety of OTL-203 in Subjects With MPS-IH Compared With Standard of Care With Allogeneic HSCTWho this might be right forMPS-IH (Hurler Syndrome) Orchard Therapeutics 41
Early research (Phase 1)Looking for participantsNCT05682144What this trial is testingISP-001: Sleeping Beauty Transposon-Engineered B Cells for MPS IWho this might be right forMucopolysaccharidosis IH/SMucopolysaccharidosis IS Immusoft of CA, Inc. 2
Testing effectiveness (Phase 2)Study completedNCT00176891What this trial is testingStem Cell Transplant w/Laronidase for HurlerWho this might be right forMucopolysaccharidosis IHurler Syndrome Masonic Cancer Center, University of Minnesota 25
Not applicableActive Not RecruitingNCT05634512What this trial is testingEvaluation of Intravenous Laronidase Pharmacokinetics Before and After Hematopoietic Cell Transplantation in Patients With Mucopolysaccharidosis Type IH.Who this might be right forHematopoietic Cell TransplantationMucopolysaccharidosis Type I Masonic Cancer Center, University of Minnesota 13
Not applicableEnded earlyNCT01572636What this trial is testingLaronidase (Aldurazyme TM) Enzyme Replacement Therapy With Hematopoietic Stem Cell Transplant for Hurler SyndromeWho this might be right forMucopolysaccharidosis Type IHMPS IHurler Syndrome Masonic Cancer Center, University of Minnesota 20