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Results for “MPS IIIB”

Showing 2 of 0 results

Not applicableAvailableNCT07733856
What this trial is testing

Early Access Treatment With Tralesinidase Alfa in Mucopolysaccharidosis Type IIIB (Sanfilippo Syndrome Type B)

Who this might be right for
Mucopolysaccharidosis Type IIIBMPS IIIB (Sanfilippo B Syndrome)
Spruce Biosciences
Testing effectiveness (Phase 2)Looking for participantsNCT06488924
What this trial is testing

An Open-label Phase I/II Study of JR-446 in Mucopolysaccharidosis Type IIIB

Who this might be right for
Mucopolysaccharidosis III-B
JCR Pharmaceuticals Co., Ltd. 10

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