Not applicableUnknownNCT03227042What this trial is testingA Prospective Natural History Study of Mucopolysaccharidosis Type IIIB (MPS IIIB)Who this might be right forMucopolysaccharidosis Type IIIB Allievex Corporation 44
Large-scale testing (Phase 3)Looking for participantsNCT06614894What this trial is testingAn Open Label Dose Escalation Study to Assess the Safety, Tolerability, and Pharmacologic Properties of High Dose Ambroxol Hydrochloride in Adult (≥ 18 Years of Age) Subjects With MPS IIIWho this might be right forSanfilippo SyndromeMPS3 Ozlem Goker-Alpan 10
Not applicableUnknownNCT03812055What this trial is testingCellular Pharmacodynamics of Small Molecules in Lysosomal Storage DisordersWho this might be right forLysosomal Storage Diseases Lysosomal and Rare Disorders Research and Treatment Center, Inc. 50
Not applicableLooking for participantsNCT05705674What this trial is testingThe Natural History Study of Patients With Sanfilippo Disease(s) (MPS3)Who this might be right forSanfilippo SyndromeMPS3 Lysosomal and Rare Disorders Research and Treatment Center, Inc. 6
Not applicableStudy completedNCT02493998What this trial is testingMucopolysaccharidosis Type IIIB (MPS IIIB)Who this might be right forMucopolysaccharidosis Type IIIBMucopolysaccharidosis Type 3 BMPS III B+1 more Allievex Corporation 22