Not applicableEnded earlyNCT04275479What this trial is testingDiabetes/ Endocrine Surveillance in SDSWho this might be right forShwachman-Diamond Syndrome Washington University School of Medicine 11
Not applicableLooking for participantsNCT04893954What this trial is testingProspective Study on the Consequences of Weight Loss After Bariatric Surgery on Obese Patients' Spine.Who this might be right forLow Back Pain in Obese Patients After Important Weight Loss Assistance Publique - Hôpitaux de Paris 80
Testing effectiveness (Phase 2)Active Not RecruitingNCT02061800What this trial is testingCD34+ (Malignant) Stem Cell Selection for Patients Receiving Allogenic Stem Cell TransplantWho this might be right forChronic Myeloid Leukemia (CML)Acute Myelogenous Leukemia (AML)Myelodysplastic Syndrome (MDS)+3 more Diane George 14
Large-scale testing (Phase 3)Looking for participantsNCT06056297What this trial is testingMavorixafor in Participants With Congenital and Acquired Primary Autoimmune and Idiopathic Chronic Neutropenic Disorders Who Are Experiencing Recurrent and/or Serious InfectionsWho this might be right forNeutropenia X4 Pharmaceuticals 176
Not applicableEnded earlyNCT02179359What this trial is testingHematopoietic Stem Cell Transplant for High Risk HemoglobinopathiesWho this might be right forSickle Cell DiseaseTransfusion Dependent Alpha- or Beta- ThalassemiaDiamond Blackfan Anemia+5 more Masonic Cancer Center, University of Minnesota 38
Not applicableStudy completedNCT00499070What this trial is testingAssessing Immune Function in Young Patients With Cytopenia That Did Not Respond to TreatmentWho this might be right forDyskeratosis CongenitaFanconi AnemiaMyelodysplastic Syndromes+2 more University Hospital Freiburg 119
Not applicableLooking for participantsNCT06056908What this trial is testingShwachman Diamond Syndrome Registry and StudyWho this might be right forShwachman-Diamond SyndromeShwachman-Diamond Syndrome-Like Boston Children's Hospital 5,000
Not applicableStudy completedNCT05687474What this trial is testingBaby Detect : Genomic Newborn ScreeningWho this might be right forCongenital Adrenal HyperplasiaFamilial Hyperinsulinemic Hypoglycemia 1Phosphoglucomutase 1 Deficiency+121 more Centre Hospitalier Universitaire de Liege 6,824
Not applicableStudy completedNCT05811143What this trial is testingExamining the Effects of Dorsal Column Stimulation on Pain From Lumbar Spinal Stenosis Related to Epidural Lipomatosis.Who this might be right forLipomatosisLow Back Pain University Hospitals Cleveland Medical Center 3
Testing effectiveness (Phase 2)Study completedNCT00919503What this trial is testingTreosulfan and Fludarabine Phosphate Before Donor Stem Cell Transplant in Treating Patients With Nonmalignant Inherited DisordersWho this might be right forNon-Neoplastic Hematologic and Lymphocytic Disorder Fred Hutchinson Cancer Center 98
Post-approval studies (Phase 4)Study completedNCT05797935What this trial is testingEvaluation of Changes in Pancreatic Fat Content Using Advanced MR Sequences in Diabetics on Dapagliflozin TherapyWho this might be right forPancreatic Lipomatosis Post Graduate Institute of Medical Education and Research, Chandigarh 50
Large-scale testing (Phase 3)Study completedNCT00176852What this trial is testingStem Cell Transplant for HemoglobinopathyWho this might be right forSickle Cell DiseaseThalassemiaSevere Congenital Neutropenia+2 more Masonic Cancer Center, University of Minnesota 22
Testing effectiveness (Phase 2)Active Not RecruitingNCT05351164What this trial is testingEvaluation of Safety and Efficiency of Metreleptin Treatment for Patients With Multiple Symmetric Lipomatosis (MSL)Who this might be right forLipomatosis, Multiple Symmetrical University of Michigan 4
Not applicableUnknownNCT00833599What this trial is testingImaging Lymphatic Function in Normal Subjects and in Persons With Lymphatic DisordersWho this might be right forLymphedemaLymphatic DisordersLipedema+3 more The University of Texas Health Science Center, Houston 283
Early research (Phase 1)Ended earlyNCT02231710What this trial is testingSafety Study of Gene Modified Donor T Cell Infusion After Stem Cell Transplant for Non-Malignant DiseasesWho this might be right forPrimary Immune Deficiency DisordersHemophagocytic LymphohistiocytosisInherited Bone Marrow Failure Syndrome+2 more Bellicum Pharmaceuticals 1
Testing effectiveness (Phase 2)Study completedNCT05387733What this trial is testingEvaluate the Efficacy and Safety of CBL-514 in Participants With Dercum's Disease LipomasWho this might be right forDercum's Disease Caliway Biopharmaceuticals Co., Ltd. 12
Testing effectiveness (Phase 2)Study completedNCT00004787What this trial is testingPhase II Pilot Study of Granulocyte Colony-Stimulating Factor for Inherited Bone Marrow Failure SyndromesWho this might be right forShwachman SyndromeFanconi's AnemiaDyskeratosis Congenita+1 more National Center for Research Resources (NCRR) 20
Early research (Phase 1)Study completedNCT01917708What this trial is testingBone Marrow Transplant With Abatacept for Non-Malignant DiseasesWho this might be right forHurler SyndromeFanconi AnemiaGlanzmann Thrombasthenia+12 more Emory University 10
Testing effectiveness (Phase 2)Study completedNCT03492840What this trial is testingTreatment of Women With Lipedema Involving Substantial Fat Knee of Women and Men With Nodular Dercum's DiseaseWho this might be right forLipedemaDercum Disease Raziel Therapeutics Ltd. 12
Testing effectiveness (Phase 2)Active Not RecruitingNCT04965597What this trial is testingTreosulfan-Based Conditioning Regimen Before a Blood or Bone Marrow Transplant for the Treatment of Bone Marrow Failure Diseases (BMT CTN 1904)Who this might be right forBone Marrow Failure SyndromeCongenital Amegakaryocytic ThrombocytopeniaDiamond-Blackfan Anemia+6 more Fred Hutchinson Cancer Center 40