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Results for “Marchiafava-Micheli Syndrome”

179 trials

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Showing 20 of 179 results

Large-scale testing (Phase 3)Study completedNCT03406507
What this trial is testing

Ravulizumab (ALXN1210) in Children and Adolescents With Paroxysmal Nocturnal Hemoglobinuria

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Alexion Pharmaceuticals, Inc. 13
Early research (Phase 1)Looking for participantsNCT07152288
What this trial is testing

Investigation of Pharmacokinetics,Safety,and Pharmacodynamics of HSK39297 in Subjects With Hepatic Impairment

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Haisco Pharmaceutical Group Co., Ltd. 24
Large-scale testing (Phase 3)Study completedNCT04463056
What this trial is testing

Efficacy and Safety of Elizaria® vs. Soliris® in Patients With PNH

Who this might be right for
Paroxysmal Nocturnal HemoglobinuriaMarchiafava-Micheli SyndromeParoxysmal Hemoglobinuria
AO GENERIUM 32
Large-scale testing (Phase 3)Not Yet RecruitingNCT07177859
What this trial is testing

A Phase III Study of NTQ5082 Capsules in the Treatment of Paroxysmal Nocturnal Hemoglobinuria Patients

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Nanjing Chia-tai Tianqing Pharmaceutical 78
Testing effectiveness (Phase 2)Active Not RecruitingNCT05876312
What this trial is testing

Safety, Tolerability, PK and PD of ADX-038 in Healthy Participants and Paroxysmal Nocturnal Hemoglobinuria (PNH) Patients

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria (PNH)
ADARx Pharmaceuticals, Inc. 50
Not applicableStudy completedNCT06154512
What this trial is testing

A Real-world, Multi-center, Prospective, Observational Study for PNH in China

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
AstraZeneca 724
Not applicableEnded earlyNCT02179359
What this trial is testing

Hematopoietic Stem Cell Transplant for High Risk Hemoglobinopathies

Who this might be right for
Sickle Cell DiseaseTransfusion Dependent Alpha- or Beta- ThalassemiaDiamond Blackfan Anemia+5 more
Masonic Cancer Center, University of Minnesota 38
Large-scale testing (Phase 3)Looking for participantsNCT06934967
What this trial is testing

Study to Assess the Pharmacokinetics, Safety, and Tolerability of Iptacopan in Pediatric PNH Patients

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Novartis Pharmaceuticals 12
Large-scale testing (Phase 3)Active Not RecruitingNCT04654468
What this trial is testing

A Study Evaluating the Efficacy, Safety, Pharmacokinetics and Pharmacodynamics of Crovalimab in Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH) Not Previously Treated With Complement Inhibition

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Hoffmann-La Roche 51
Large-scale testing (Phase 3)Study completedNCT06799546
What this trial is testing

A Phase III Study to Evaluate the Efficacy and Safety of HSK39297 in Patients With Paroxysmal Nocturnal Hemoglobinuria Who Are Naive to Complement Inhibitor Therapy

Who this might be right for
PNH
Haisco Pharmaceutical Group Co., Ltd. 73
Large-scale testing (Phase 3)Study completedNCT00122304
What this trial is testing

Study of Safety in Hemolytic Paroxysmal Nocturnal Hemoglobinuria (PNH) Patients Treated With Eculizumab

Who this might be right for
Hemoglobinuria, Paroxysmal
Alexion Pharmaceuticals, Inc. 85
Large-scale testing (Phase 3)Not Yet RecruitingNCT07177872
What this trial is testing

A Long-term Efficacy and Safety of NTQ5082 Capsules

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Nanjing Chia-tai Tianqing Pharmaceutical 78
Not applicableStudy completedNCT01020188
What this trial is testing

Study of Global Coagulation Tests in Patients With Paroxysmal Nocturnal Haemoglobinuria

Who this might be right for
Paroxysmal Nocturnal Haemoglobinuria
King's College Hospital NHS Trust 60
Testing effectiveness (Phase 2)Study completedNCT04888507
What this trial is testing

Pozelimab and Cemdisiran Combination Therapy in Adult Participants With Paroxysmal Nocturnal Hemoglobinuria Who Switch From Eculizumab Therapy

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Regeneron Pharmaceuticals 6
Testing effectiveness (Phase 2)Looking for participantsNCT06978699
What this trial is testing

A Phase II Study Evaluating the Efficacy and Safety of XH-S003 Capsules in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)

Who this might be right for
PNH - Paroxysmal Nocturnal Hemoglobinuria
S-INFINITY Pharmaceuticals Co., Ltd 24
Not applicableNot Yet RecruitingNCT06848296
What this trial is testing

Evaluate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics and Preliminary Efficacy of of VSA012 in Subjects with Paroxysmal Nocturnal Hemoglobinuria(PNH)

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Visirna Therapeutics HK Limited 16
Testing effectiveness (Phase 2)Active Not RecruitingNCT06238544
What this trial is testing

Long-term Safety and Tolerability of HRS-5965 in Patients With Paroxysmal Nocturnal Hemoglobinuria

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Chengdu Suncadia Medicine Co., Ltd. 132
Not applicableStudy completedNCT04128943
What this trial is testing

Electronic Patient-reported Outcome Monitoring in Aplastic Anemia and Paroxysmal Nocturnal Hemoglobinuria

Who this might be right for
Aplastic AnemiaParoxysmal Nocturnal Hemoglobinuria
University Hospital, Basel, Switzerland 9
Not applicableNot Yet RecruitingNCT07108023
What this trial is testing

Hematological Disorders in EHPVO Patients

Who this might be right for
Extrahepatic Portal Vein Obstruction (EHPVO)ThrombophiliaMyeloproliferative Neoplasms (MPN)+5 more
Rahab Nady 115
Early research (Phase 1)Study completedNCT02264639
What this trial is testing

A Phase I Study to Assess the Safety of Pegcetacoplan (APL-2) as an Add-On to Standard of Care in Subjects With PNH

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Apellis Pharmaceuticals, Inc. 9
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