Crick
HomeTrialsGenesDrugs23andMeGraphBlogContact
  • Home
  • Trials
  • Genes
  • Drugs
  • 23andMe
  • Graph
  • Blog
  • Contact
Crick

An open-source clinical intelligence platform. Explore clinical trials, gene networks, and molecular structures using public data sources.

Data Sources

  • ClinicalTrials.gov
  • OpenTargets
  • ClinVar
  • PubChem

Links

  • Contact
  • Privacy

© 2026 Crick. All rights reserved.

Crick is for educational purposes only. Not medical advice.

Results for “Mucopolysaccharidosis Disorders”

309 trials

Filters

Phase
Early Phase 1
Phase 1
Phase 2
Phase 3
Phase 4
Status
Recruiting
Active, Not Recruiting
Not Yet Recruiting
Completed
Enrolling by Invitation

Showing 20 of 309 results

Testing effectiveness (Phase 2)Enrolling By InvitationNCT07393373
What this trial is testing

Open-Label, Long-Term, Extension Study of Infigratinib in Children With Hypochondroplasia

Who this might be right for
Hypochondroplasia
QED Therapeutics, a BridgeBio company 135
Testing effectiveness (Phase 2)Ended earlyNCT05116046
What this trial is testing

Continuation Study of Long-term Safety, Tolerability, Pharmacokinetics and Efficacy of Recifercept in Achondroplasia

Who this might be right for
Achondroplasia
Pfizer 35
Not applicableNot Yet RecruitingNCT07516587
What this trial is testing

Study to Investigate the Efficacy of a Digestive Health Dietary Supplement on Post-meal Bloating in Healthy Participants

Who this might be right for
Digestive HealthAbdominal DiscomfortGas and Bloating
Arrae 100
Testing effectiveness (Phase 2)Study completedNCT03406962
What this trial is testing

MGTA-456 in Patients With Inherited Metabolic Disorders Undergoing Hematopoietic Stem Cell Transplantation (HSCT)

Who this might be right for
Inherited Metabolic Disorders (IMD)
Magenta Therapeutics, Inc. 8
Post-approval studies (Phase 4)Study completedNCT00299000
What this trial is testing

Two Dose Level Study of Naglazyme(TM) (Galsulfase) in Infants With MPS VI

Who this might be right for
Mucopolysaccharidosis VIMaroteaux-Lamy Syndrome
BioMarin Pharmaceutical 4
Not applicableStudy completedNCT04035811
What this trial is testing

Prospective Clinical Assessment Study in Children With Achondroplasia (ACH)

Who this might be right for
Achondroplasia
QED Therapeutics, a BridgeBio company 271
Not applicableStudy completedNCT03292887
What this trial is testing

Hunter Outcome Survey (HOS)

Who this might be right for
Hunter Syndrome
Shire 1,443
Not applicableStudy completedNCT01047306
What this trial is testing

Patients With Sanfilippo Syndrome Type A (MPS IIIA)

Who this might be right for
Sanfilippo Syndrome Type A
Shire 25
Post-approval studies (Phase 4)Study completedNCT02455622
What this trial is testing

Long-term Evaluation on Height and Weight in Patients With MPS II Who Started Treatment at < 6 Years of Age

Who this might be right for
Hunter Syndrome
Shire 21
Not applicableStudy completedNCT03529786
What this trial is testing

Mucopolysaccharidosis Type II Natural History

Who this might be right for
Mucopolysaccharidosis II
REGENXBIO Inc. 36
Not applicableAvailableNCT07733856
What this trial is testing

Early Access Treatment With Tralesinidase Alfa in Mucopolysaccharidosis Type IIIB (Sanfilippo Syndrome Type B)

Who this might be right for
Mucopolysaccharidosis Type IIIBMPS IIIB (Sanfilippo B Syndrome)
Spruce Biosciences
Large-scale testing (Phase 3)Active Not RecruitingNCT06031259
What this trial is testing

Extension Study of Idursulfase-IT Along With Elaprase in Children and Adults With Hunter Syndrome and Cognitive Impairment

Who this might be right for
Hunter Syndrome
Takeda 6
Not applicableStudy completedNCT03150069
What this trial is testing

Pregnancy With Morquio Syndrome - What Are Patients' Perspectives and Has ERT Changed Them?

Who this might be right for
Morquio DiseaseMPS - Mucopolysaccharidosis
Emory University 18
Testing effectiveness (Phase 2)UnknownNCT03632213
What this trial is testing

Evaluation of Losartan on Cardiovascular Disease in Patients With Mucopolysaccharidoses IV A and VI

Who this might be right for
Mucopolysaccharidosis IV AMucopolysaccharidosis VIMucopolysaccharidoses+6 more
Hospital de Clinicas de Porto Alegre 10
Post-approval studies (Phase 4)Enrolling By InvitationNCT05492799
What this trial is testing

Safety, Tolerability and Efficacy of ICV AX 250 Treatment in MPS IIIB -OLE

Who this might be right for
MPS III B
Allievex Corporation 15
Not applicableStudy completedNCT07230821
What this trial is testing

Radicle GI Health RDH™: A Study Assessing the Impact of Health and Wellness Products on Gastrointestinal (GI) Health and Related Health Outcomes

Who this might be right for
Gas and BloatingDiarrheaConstipation
Radicle Science 500
Not applicableEnded earlyNCT01733615
What this trial is testing

Discovering New Biomarkers For Monitoring Disease Progression in Patients With Mucopolysaccharidosis IVA

Who this might be right for
Mucopolysaccharidosis Type IVA
Emory University 3
Not applicableNot Yet RecruitingNCT07136896
What this trial is testing

Nutritional Assessment in Patient of Mucopolysaccharide "

Who this might be right for
Mucopolysaccharidosis (MPS)Malnutrition (Calorie)Undernutrition
Assiut University 40
Not applicableStudy completedNCT03582449
What this trial is testing

Intensive Pharmacovigilance Program for Elaprase (SHP ELA-701)

Who this might be right for
Hunter Syndrome
Shire 5
Not applicableLooking for participantsNCT05876416
What this trial is testing

Decoding the Genetic Landscape of Skeletal Diseases

Who this might be right for
Genetic Skeletal DiseasesSkeletal DysplasiaMolecular Causes+1 more
Karolinska Institutet 450
Next Page