Not applicableStudy completedNCT04186260What this trial is testingA Gender and Culturally Specific Approach to Reduce NAFLD in Mexican-American MenWho this might be right forNAFLD University of Arizona 15
Testing effectiveness (Phase 2)Study completedNCT05267262What this trial is testingStudy to Evaluate R3R01 in Patients With Alport Syndrome and Patients With Focal Segmental GlomerulosclerosisWho this might be right forAlport SyndromeFocal Segmental Glomerulosclerosis River 3 Renal Corp. 43
Testing effectiveness (Phase 2)Study completedNCT00579527What this trial is testingPhase I/II Thymus Transplantation With Immunosuppression #950Who this might be right forDiGeorge AnomalyComplete DiGeorge AnomalyComplete Atypical DiGeorge Anomaly+2 more Sumitomo Pharma Switzerland GmbH 14
Testing effectiveness (Phase 2)Study completedNCT02047318What this trial is testingAn Extension Study to Evaluate the Long-Term Safety and Durability of Effect of LUM001 in the Treatment of Cholestatic Liver Disease in Subjects With Alagille Syndrome (ALGS)Who this might be right forAlagille Syndrome Mirum Pharmaceuticals, Inc. 19
Not applicableEnrolling By InvitationNCT06330324What this trial is testingReproductive Options in Inherited Skin DiseasesWho this might be right forIchthyosisPalmoplantar KeratosesEpidermolysis Bullosa+7 more Maastricht University Medical Center 650
Early research (Phase 1)WithdrawnNCT02831179What this trial is testingVeliparib, Capecitabine, and Temozolomide in Patients With Advanced, Metastatic, and Recurrent Neuroendocrine TumorWho this might be right forFunctional Pancreatic Neuroendocrine TumorMalignant SomatostatinomaMerkel Cell Carcinoma+26 more Vanderbilt-Ingram Cancer Center
Post-approval studies (Phase 4)Study completedNCT05458479What this trial is testingFluoxetine Treatment of Depression in Down SyndromeWho this might be right forDown SyndromeDepression Massachusetts General Hospital 4
Large-scale testing (Phase 3)Study completedNCT01594346What this trial is testingMulticenter Vitamin E Trial in Aging Persons With Down SyndromeWho this might be right forAlzheimer's DiseaseDown Syndrome New York State Institute for Basic Research 349
Not applicableLooking for participantsNCT03704207What this trial is testingUtility of PCD Diagnostics to Improve Clinical CareWho this might be right forPrimary Ciliary Dyskinesia Vanderbilt University Medical Center 200
Testing effectiveness (Phase 2)Study completedNCT00031434What this trial is testingValganciclovir in Congenital CMV InfantsWho this might be right forCytomegalovirus Infections National Institute of Allergy and Infectious Diseases (NIAID) 24
Not applicableStudy completedNCT04319107What this trial is testingClassifying Ectopia Lentis in Marfan Syndrome Into Five Grades of Increasing SeverityWho this might be right forMarfan SyndromeEctopia Lentis Hospices Civils de Lyon 110
Large-scale testing (Phase 3)Study completedNCT01270971What this trial is testingEfficacy and Safety Evaluation of AN2690 Topical Solution to Treat Onychomycosis of the ToenailWho this might be right forOnychomycosis of Toenails Pfizer 594
Testing effectiveness (Phase 2)Study completedNCT01469832What this trial is testingSafety and Tolerability of Sub-retinal Transplantation of Human Embryonic Stem Cell Derived Retinal Pigmented Epithelial (hESC-RPE) Cells in Patients With Stargardt's Macular Dystrophy (SMD)Who this might be right forStargardt's Macular Dystrophy Astellas Institute for Regenerative Medicine 12
Not applicableStudy completedNCT03876301What this trial is testingLead-in Study to Collect Prospective Efficacy and Safety Data of Current FVIII Prophylaxis Replacement Therapy in Adult Hemophilia A ParticipantsWho this might be right forBlood Coagulation DisorderBlood Coagulation Disorders, InheritedCoagulation Protein Disorders+6 more Spark Therapeutics, Inc. 25
Early research (Phase 1)Study completedNCT05718921What this trial is testingA Safety, Tolerability and Pharmacokinetics Study of Topical Ointment YR001 in Adult Healthy VolunteersWho this might be right forAtopic DermatitisPsoriasis Hangzhou Yirui Pharmaceutical Technology Co., Ltd 54
Not applicableEnded earlyNCT00651716What this trial is testingT Cells in Predicting Acute Graft-Versus-Host Disease in Patients Undergoing Donor Stem Cell TransplantWho this might be right forBreast CancerChronic Myeloproliferative DisordersGestational Trophoblastic Tumor+8 more Vanderbilt-Ingram Cancer Center 150
Early research (Phase 1)Study completedNCT06117020What this trial is testingSingle and Multiple Ascending Dose Study of MTR-601 in Healthy IndividualsWho this might be right forMuscle SpasticityHypertonia, MuscleCerebral Palsy+5 more Motric Bio 89
Testing effectiveness (Phase 2)Looking for participantsNCT07557446What this trial is testingA Dose REgimen-Finding Study of AGA2115 in Chinese Patients With Osteogenesis ImpeRfecta (EIR)Who this might be right forOsteogenesis Imperfecta (OI) Angitia Biopharmaceuticals Guangzhou Limited 48
Not applicableStudy completedNCT01135888What this trial is testingShort Term Effects and Risks of Physical Exercise in Subjects With Hypohidrotic Ectodermal DysplasiaWho this might be right forX-Linked Hypohidrotic Ectodermal DysplasiaExercise-induced Rise of Body Temperature University Hospital Erlangen 28
Not applicableStudy completedNCT01597063What this trial is testingClinical Evaluation of the SEQureDx Trisomy Test in Low Risk PregnanciesWho this might be right forAneuploidyDown SyndromeNoninvasive Prenatal Screening Sequenom, Inc. 3,333