Not applicableLooking for participantsNCT00313677What this trial is testingClinical Trial Readiness for the DystroglycanopathiesWho this might be right forMuscular Dystrophy Katherine Mathews 190
Early research (Phase 1)Ended earlyNCT04784390What this trial is testingProof of Concept Study of Binocular Videogames Versus Patching for AmblyopiaWho this might be right forAmblyopia Novartis Pharmaceuticals 27
Testing effectiveness (Phase 2)UnknownNCT03944447What this trial is testingOutcomes Mandate National Integration With Cannabis as MedicineWho this might be right forChronic PainChronic Pain SyndromeChronic Pain Due to Injury+30 more OMNI Medical Services, LLC 200,000
Not applicableEnded earlyNCT03886753What this trial is testingPharmacokinetic (PK) and Pharmacodynamics (PD) Study of Ilera Specific ProductsWho this might be right forALSAutism Spectrum DisorderCancer+15 more Children's Hospital of Philadelphia 10
Not applicableStudy completedNCT01505569What this trial is testingAuto Transplant for High Risk or Relapsed Solid or CNS TumorsWho this might be right forEwing's Family TumorsRenal TumorsHepatoblastoma+9 more Masonic Cancer Center, University of Minnesota 44
Testing effectiveness (Phase 2)Study completedNCT02023866What this trial is testingOpen-Label, Dose-Escalating Study Assessing Safety, Tolerability, Efficacy, of RP103 in Mitochondrial DiseaseWho this might be right forInherited Mitochondrial Disease, Including Leigh Syndrome Amgen 36
Not applicableLooking for participantsNCT05635266What this trial is testingTissue Repository Providing Annotated Biospecimens for Approved Investigator-directed Biomedical Research InitiativesWho this might be right forAge-Related Macular DegenerationAllergiesAlpha-Gal Syndrome+44 more Sanguine Biosciences 20,000
Not applicableStudy completedNCT06180421What this trial is testingMitochondrial Video Assessment Source Material StudyWho this might be right forPolG, Primary Mitochondrial Myopathy The Emmes Company, LLC 28
Early research (Phase 1)Study completedNCT00638898What this trial is testingBusulfan, Melphalan, Topotecan Hydrochloride, and a Stem Cell Transplant in Treating Patients With Newly Diagnosed or Relapsed Solid TumorWho this might be right forSolid TumorAdult Central Nervous System Germ Cell TumorAdult Rhabdomyosarcoma+27 more City of Hope Medical Center 25
Testing effectiveness (Phase 2)Study completedNCT05199584What this trial is testingA Study Evaluating the Safety and Efficacy of ENV-101 (Taladegib) in Patients With Advanced Solid Tumors Harboring PTCH1 Loss of Function MutationsWho this might be right forSolid Tumors With PTCH1 Loss-of-function Mutations Endeavor Biomedicines, Inc. 20
Not applicableStudy completedNCT00210431What this trial is testingPost Marketing Surveillance Study of DysportWho this might be right forBlepharospasmHemifacial SpasmCervical Dystonia+6 more Ipsen 783
Not applicableLooking for participantsNCT05554835What this trial is testingGlobal Registry and Natural History Study for Mitochondrial DisordersWho this might be right forMitochondrial DiseasesKearns-Sayre SyndromeMIDD+15 more LMU Klinikum 6,000
Testing effectiveness (Phase 2)Looking for participantsNCT06350110What this trial is testingFourth-gen CAR T Cells Targeting BCMA/CD19 for Refractory Systemic Lupus Erythematosus (SLE)Who this might be right forSystemic Lupus ErythematosusLupus NephritisAutoimmune Diseases+6 more Essen Biotech 75
Not applicableLooking for participantsNCT01694940What this trial is testingNorth American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)Who this might be right forMitochondrial DisordersMitochondrial Genetic DisordersMitochondrial Diseases+2 more Columbia University 1,000
Not applicableLooking for participantsNCT01238250What this trial is testingOnline Study of People Who Have Genetic Changes and Features of Autism: Simons SearchlightWho this might be right for16P11.2 Deletion Syndrome16p11.2 Duplications1Q21.1 Deletion+181 more Simons Searchlight 100,000
Testing effectiveness (Phase 2)Ended earlyNCT02473445What this trial is testingA Long-term Extension of Study RP103-MITO-001 (NCT02023866) to Assess Cysteamine Bitartrate Delayed-release Capsules (RP103) in Children With Inherited Mitochondrial DiseaseWho this might be right forMitochondrial Diseases Amgen 22
Early research (Phase 1)Study completedNCT03888716What this trial is testingA Phase Ia/Ib, SAD and MAD Study of of KL1333 in Healthy Subjects and Patients With Primary Mitochondrial DiseaseWho this might be right forMitochondrial DiseasesMitochondrial Respiratory Chain DeficienciesMELAS Syndrome+1 more Abliva AB 72
Not applicableStudy completedNCT03432871What this trial is testingNicotinamide Riboside and Mitochondrial BiogenesisWho this might be right forMitochondrial DiseasesMitochondrial MyopathiesProgressive External Ophthalmoplegia+4 more Cambridge University Hospitals NHS Foundation Trust 13
Not applicableStudy completedNCT01431326What this trial is testingPharmacokinetics of Understudied Drugs Administered to Children Per Standard of CareWho this might be right forAdenovirusAnesthesiaAnxiety+56 more Daniel Benjamin 3,520
Not applicableLooking for participantsNCT07136844What this trial is testingGait Analysis Parameter and Upper Limb Evaluation in Adult Patients With Neurological or Metabolic PathologyWho this might be right forNeuromuscular DiseasesObesity (Disorder)Myotonic Dystrophy 1+9 more Centre Hospitalier Universitaire de Liege 300