Not applicableLooking for participantsNCT03333200What this trial is testingLongitudinal Study of Neurodegenerative DisordersWho this might be right forMLDKrabbe DiseaseALD+24 more University of Pittsburgh 1,500
Early research (Phase 1)Study completedNCT01705990What this trial is testingSafety and Immunogenicity Study of SeV-G(NP) HIV Vaccine Administered Intranasally and Ad35-GRIN HIV Vaccine Given Intramuscularly in Prime-Boost Regimens in HIV-Uninfected VolunteersWho this might be right forHIV Infections International AIDS Vaccine Initiative 65
Testing effectiveness (Phase 2)WithdrawnNCT01183455What this trial is testingA Research Trial of Aralast NP in New Onset Diabetes (RETAIN) - Part IIWho this might be right forDiabetes Mellitus, Type 1 National Institute of Allergy and Infectious Diseases (NIAID)
Early research (Phase 1)Study completedNCT00008450What this trial is testingTotal-Body Irradiation Followed By Cyclosporine and Mycophenolate Mofetil in Treating Patients With Severe Combined Immunodeficiency Undergoing Donor Bone Marrow TransplantWho this might be right forAdenosine Deaminase DeficiencyAutosomal Recessive DisorderImmune System Disorder+4 more Fred Hutchinson Cancer Center 6
Post-approval studies (Phase 4)WithdrawnNCT04440488What this trial is testingARALAST NP Alpha-1 Lung Density Chronic Obstructive Pulmonary Disease-Emphysema (COPD-E) StudyWho this might be right forChronic Obstructive Pulmonary DiseaseAlpha1-antitrypsin Deficiency Shire
Large-scale testing (Phase 3)Ended earlyNCT02722304What this trial is testingStage 1 Study of ARALAST NP and GLASSIA in A1PI DeficiencyWho this might be right forChronic Obstructive Pulmonary DiseaseAlpha1-antitrypsin Deficiency Baxalta now part of Shire 7
Early research (Phase 1)Ended earlyNCT01183468What this trial is testingA Research Trial of Aralast in New Onset Diabetes (RETAIN)Who this might be right forDiabetes Mellitus, Type 1 National Institute of Allergy and Infectious Diseases (NIAID) 17
Early research (Phase 1)Study completedNCT05781542What this trial is testingClinical Trial to Evaluate the Safety and Immunogenicity of Synthetic DNAs Encoding NP-GT8 and IL-12, With or Without a TLR-agonist-Adjuvanted HIV Env Trimer 4571 Boost, in Adults Without HIVWho this might be right forHIV Infections National Institute of Allergy and Infectious Diseases (NIAID) 46
Post-approval studies (Phase 4)WithdrawnNCT05466747What this trial is testingRYMPHYSIA for Alpha1-Proteinase Inhibitor (A1PI) Therapy in Adults With A1PI Deficiency and Chronic Obstructive Pulmonary Disease (COPD)-EmphysemaWho this might be right forChronic Obstructive Pulmonary Disease (COPD)Alpha1-Antitrypsin Deficiency Takeda
Not applicableLooking for participantsNCT06092346What this trial is testingA Natural History Study Seeks to Understand the Clinical, Genomic, Pharmacological, Laboratory, and Dietary Determinates of Pyrimidine and Purine Metabolism DisordersWho this might be right forAMPD3, OMIM*102772, AMP Deaminase DeficiencyAK1, OMIM *103000, Adenylate Kinase DeficiencyAMPD1, OMIM *102770, Myopathy Due to Myoadenylate Deaminase Deficiency+25 more National Human Genome Research Institute (NHGRI)