Post-approval studies (Phase 4)Ended earlyNCT03726996What this trial is testingDesipramine in Infantile Neuroaxonal Dystrophy (INAD).Who this might be right forInfantile Neuroaxonal Dystrophy Duke University 4
Large-scale testing (Phase 3)Active Not RecruitingNCT03570931What this trial is testingAssess Efficacy and Safety of RT001 in Subjects With Infantile Neuroaxonal DystrophyWho this might be right forInfantile Neuroaxonal Dystrophy Biojiva LLC 19
Not applicableLooking for participantsNCT06596746What this trial is testingNeurodegenerative Diseases Progression Markers (MARKERS-NDD)Who this might be right forNeurodegenerative DiseasesParkinson DiseaseSynucleinopathies+15 more Casa di Cura San Raffaele Cassino 600
Not applicableStudy completedNCT03999814What this trial is testingNatural History of Infantile Neuroaxonal DystrophyWho this might be right forInfantile Neuroaxonal DystrophyINAD Biojiva LLC 13
Not applicableUnknownNCT05440994What this trial is testingPhenotypic Description of Patients With Atypical Clinical Forms of PLA2G6 MutationsWho this might be right forNeuroaxonal Dystrophy, Atypical University Hospital, Clermont-Ferrand 20
Not applicableStudy completedNCT04027816What this trial is testingA Natural History Study of Infantile Neuroaxonal DystrophyWho this might be right forNeuroaxonal Dystrophy, Infantile Biojiva LLC 43
Not applicableUnknownNCT04319796What this trial is testingEuropean Registry on Rare Neurological DiseasesWho this might be right forRare Diseases University Hospital Tuebingen 5,000