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Results for “Neurodegenerative Disease, Hereditary”

2,163 trials

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Showing 20 of 2,163 results

Not applicableLooking for participantsNCT06610019
What this trial is testing

Cardiovascular Multimodality Imaging Study

Who this might be right for
Non-ischemic CardiomyopathyCardiomyopathiesHypertrophic Cardiomyopathy+7 more
Montefiore Medical Center 5,000
Testing effectiveness (Phase 2)Study completedNCT01412151
What this trial is testing

Creatine Safety & Tolerability in Huntington's Disease

Who this might be right for
Huntington's Disease (HD)
Massachusetts General Hospital 10
Testing effectiveness (Phase 2)Active Not RecruitingNCT04980872
What this trial is testing

The Safety and Tolerability in Participants With PIK3CA-related Overgrowth Spectrum or Proteus Syndrome Who Are Being Treated With Miransertib (MK-7075) in Other Studies (MK-7075-006)

Who this might be right for
PIK3CA-Related Overgrowth Spectrum (PROS)/Proteus Syndrome (PS)
Merck Sharp & Dohme LLC 60
Not applicableLooking for participantsNCT02855476
What this trial is testing

HDClarity: a Multi-site Cerebrospinal Fluid Collection Initiative to Facilitate Therapeutic Development for Huntington's Disease

Who this might be right for
Huntington's Disease
University College, London 2,500
Not applicableNo Longer AvailableNCT04381091
What this trial is testing

Expanded Access Program for Idebenone in Patients With Leber's Hereditary Optic Neuropathy Who Completed the LEROS Study

Who this might be right for
Leber's Hereditary Optic Neuropathy
Santhera Pharmaceuticals
Not applicableLooking for participantsNCT07213648
What this trial is testing

Modification of Threat Interpretation Bias to Reduce Anxiety in Neurodegenerative Movement Disorders (Aim 3)

Who this might be right for
Huntington DiseaseParkinson Disease
University of Virginia 136
Not applicableLooking for participantsNCT05522374
What this trial is testing

TIRCON International NBIA Registry

Who this might be right for
Neurodegeneration With Brain Iron Accumulation (NBIA)Pantothenate Kinase-associated Neurodegeneration (PKAN)Beta-Propeller Protein-Associated Neurodegeneration (BPAN)+8 more
LMU Klinikum 2,000
Not applicableEnded earlyNCT04076852
What this trial is testing

Gilles de la Tourette Syndrome (TS) and Seasonality

Who this might be right for
Tourette Syndrome
I.R.C.C.S Ospedale Galeazzi-Sant'Ambrogio 39
Not applicableStudy completedNCT01451463
What this trial is testing

Impact of Xenazine(Tetrabenazine)on Gait and Functional Activity in Individuals With Huntington's Disease

Who this might be right for
Huntington's Disease
Ohio State University 11
Not applicableUnknownNCT02403258
What this trial is testing

The Effect and Safety of Plum-blossom Needle for Tourette Syndrome

Who this might be right for
Tourette Syndrome
Guang'anmen Hospital of China Academy of Chinese Medical Sciences 60
Testing effectiveness (Phase 2)Looking for participantsNCT06185764
What this trial is testing

VX-670 in Adult Participants With Myotonic Dystrophy 1 (DM1)

Who this might be right for
Myotonic Dystrophy Type 1 (DM1)
Vertex Pharmaceuticals Incorporated 36
Not applicableStudy completedNCT03018184
What this trial is testing

Contractile Cross Sectional Areas and Muscle Strength in Patients With Congenital Myopathies

Who this might be right for
Inherited Muscle DiseasesCongenital MyopathyRYR1-myopathy
Rigshospitalet, Denmark 31
Testing effectiveness (Phase 2)Active Not RecruitingNCT03190915
What this trial is testing

Trametinib in Treating Patients With Relapsed or Refractory Juvenile Myelomonocytic Leukemia

Who this might be right for
Juvenile Myelomonocytic LeukemiaNeurofibromatosis Type 1
National Cancer Institute (NCI) 10
Not applicableNot Yet RecruitingNCT06663878
What this trial is testing

An Exploratory Study to Evaluate the Tolerability and Safety of MWAV201 in Subjects With Wilson Disease

Who this might be right for
Wilson Disease
Xinhua Hospital, Shanghai Jiao Tong University School of Medicine 9
Large-scale testing (Phase 3)Study completedNCT03837184
What this trial is testing

Single-Dose Gene Replacement Therapy Using for Patients With Spinal Muscular Atrophy Type 1 With One or Two SMN2 Copies

Who this might be right for
Spinal Muscular Atrophy Type I
Novartis Gene Therapies 2
Not applicableLooking for participantsNCT07092358
What this trial is testing

Hereditary Ataxia Research on Multi-Omics and Neuroclinical Insights in the Yangtze Delta

Who this might be right for
Hereditary Ataxia
Second Affiliated Hospital, School of Medicine, Zhejiang University 5,000
Testing effectiveness (Phase 2)Study completedNCT02247206
What this trial is testing

VoIP Delivered Behavior Therapy for Tourette Syndrome

Who this might be right for
Tourette SyndromeChronic Tic Disorder
University of Wisconsin, Milwaukee 20
Not applicableLooking for participantsNCT06747884
What this trial is testing

Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension

Who this might be right for
Congenital Myotonic DystrophyChildhood Myotonic DystrophyMyotonic Dystrophy
Virginia Commonwealth University 200
Post-approval studies (Phase 4)Study completedNCT05073133
What this trial is testing

Safety and Efficacy of Intravenous OAV101 (AVXS-101) in Pediatric Patients With Spinal Muscular Atrophy (SMA) (OFELIA)

Who this might be right for
Muscular Atrophy, Spinal
Novartis Pharmaceuticals 16
Early research (Phase 1)Study completedNCT00990613
What this trial is testing

A Study Evaluating The Absorption Of Dimebon Into The Body From A Dimebon Solution Applied To The Skin

Who this might be right for
Alzheimer's DiseaseHuntington's Disease
Pfizer 19
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