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Results for “Neuronal Ceroid Lipofuscinosis CLN3”

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Showing 13 of 0 results

Early research (Phase 1)Study completedNCT01161576
What this trial is testing

Safety Study of a Gene Transfer Vector (Rh.10) for Children With Late Infantile Neuronal Ceroid Lipofuscinosis (LINCL)

Who this might be right for
Batten DiseaseLate-Infantile Neuronal Ceroid Lipofuscinosis
Weill Medical College of Cornell University 12
Not applicableLooking for participantsNCT03307304
What this trial is testing

Investigations of Juvenile Neuronal Ceroid Lipofuscinosis

Who this might be right for
Juvenile Neuronal Ceroid Lipofuscinosis (CLN3)Batten Disease
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) 300
Not applicableActive Not RecruitingNCT04273243
What this trial is testing

Long-Term Follow Up of CLN6 Batten Disease Subjects Following Gene Transfer

Who this might be right for
CLN6Batten Disease
Emily de los Reyes 10
Testing effectiveness (Phase 2)Study completedNCT05174039
What this trial is testing

An Open-label Safety, Pharmacokinetic, and Efficacy Study of Miglustat for the Treatment of Subjects With Batten Ceroid Lipofuscinosis, Neuronal 3 (CLN3) Disease

Who this might be right for
Batten Disease
Beyond Batten Disease Foundation 6
Testing effectiveness (Phase 2)Study completedNCT01414985
What this trial is testing

AAVRh.10 Administered to Children With Late Infantile Neuronal Ceroid Lipofuscinosis

Who this might be right for
Late Infantile Neuronal Ceroid LipofuscinosisBatten Disease
Weill Medical College of Cornell University 8
Testing effectiveness (Phase 2)Study completedNCT01907087
What this trial is testing

A Phase 1/2 Open-Label Dose-Escalation Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Efficacy of Intracerebroventricular BMN 190 in Patients With Late-Infantile Neuronal Ceroid Lipofuscinosis (CLN2) Disease

Who this might be right for
Jansky-Bielschowsky DiseaseBatten DiseaseLate-Infantile Neuronal Ceroid Lipofuscinosis Type 2+1 more
BioMarin Pharmaceutical 24
Testing effectiveness (Phase 2)Active Not RecruitingNCT05228145
What this trial is testing

Gene Therapy Study for Children With CLN5 Batten Disease

Who this might be right for
Neuronal Ceroid Lipofuscinosis CLN5
Neurogene Inc. 6
Early research (Phase 1)Study completedNCT00337636
What this trial is testing

Study of HuCNS-SC Cells in Patients With Infantile or Late Infantile Neuronal Ceroid Lipofuscinosis (NCL)

Who this might be right for
Neuronal Ceroid Lipofuscinosis
StemCells, Inc. 6
Not applicableStudy completedNCT05642221
What this trial is testing

Functional Near-Infrared Spectroscopy (fNIRS) Combined With Diffuse Correlation Spectroscopy (DCS) in Neurocognitive Disease as Compared to Healthy Neurotypical Controls

Who this might be right for
Juvenile Neuronal Ceroid LipofuscinosisSmith-Lemli-Opitz SyndromeCreatine Transporter Deficiency+1 more
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) 73
Not applicableEnded earlyNCT04974307
What this trial is testing

Optic-to-Audio Device in a Pediatric Cohort With CLN3-related Conditions or Low Vision

Who this might be right for
CLN3-related DisordersNon-CLN3 Related Low Vision
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) 11
Early research (Phase 1)Study completedNCT00151216
What this trial is testing

Safety Study of a Gene Transfer Vector for Children With Late Infantile Neuronal Ceroid Lipofuscinosis

Who this might be right for
Batten DiseaseLate Infantile Neuronal Ceroid Lipofuscinosis
Weill Medical College of Cornell University 10
Not applicableLooking for participantsNCT01873924
What this trial is testing

Clinical and Neuropsychological Investigations in Batten Disease

Who this might be right for
Neuronal Ceroid LipofuscinosisNeuronal Ceroid Lipofuscinosis CLN1Neuronal Ceroid Lipofuscinosis CLN2+7 more
University of Rochester 500
Not applicableStudy completedNCT01966757
What this trial is testing

Neuronal Ceroid Lipofuscinosis and Associated Sleep Abnormalities

Who this might be right for
Neuronal Ceroid LipofuscinosisBatten's Disease
Nationwide Children's Hospital 57