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Results for “Neuronopathic Gaucher Disease”

32 trials

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Showing 20 of 32 results

Not applicableStudy completedNCT00001289
What this trial is testing

Effects of Enzyme Replacement in Gaucher's Disease

Who this might be right for
Gaucher's Disease
National Institute of Neurological Disorders and Stroke (NINDS) 70
Testing effectiveness (Phase 2)Ended earlyNCT03746587
What this trial is testing

Study of Arimoclomol in Patients Diagnosed With Gaucher Disease Type 1 or 3

Who this might be right for
Gaucher Disease, Type 1Gaucher Disease, Type 3
ZevraDenmark 39
Testing effectiveness (Phase 2)Active Not RecruitingNCT02843035
What this trial is testing

Venglustat in Combination With Cerezyme in Adult Patients With Gaucher Disease Type 3 With Venglustat Monotherapy Extension

Who this might be right for
Gaucher Disease Type 1Gaucher Disease Type 3
Genzyme, a Sanofi Company 12
Not applicableLooking for participantsNCT03240653
What this trial is testing

Gaucherite - A Study to Stratify Gaucher Disease

Who this might be right for
Gaucher Disease, Type IGaucher Disease, Type III
Cambridge University Hospitals NHS Foundation Trust 250
Early research (Phase 1)Study completedNCT03159117
What this trial is testing

Pfizer PF-06688992 in Patients With Stage III or Stage IV Melanoma

Who this might be right for
Melanoma
Memorial Sloan Kettering Cancer Center 7
Testing effectiveness (Phase 2)UnknownNCT05447494
What this trial is testing

Phase 1/2 Study of CAN103 in Subjects With Gaucher Disease

Who this might be right for
Gaucher Disease, Type 1Gaucher Disease, Type 3
CANbridge (Suzhou) Bio-pharma Co., Ltd. 40
Not applicableLooking for participantsNCT05586243
What this trial is testing

MAGNETIC RESONANCE SPECTROSCOPY BIOMARKERS IN TYPE 3 GAUCHER DISEASE (GD3)

Who this might be right for
Gaucher Disease, Type 3
University of Minnesota 5
Testing effectiveness (Phase 2)Study completedNCT00358150
What this trial is testing

The Efficacy and Safety of Eliglustat Tartrate (Genz-112638) in Type 1 Gaucher Patients

Who this might be right for
Gaucher Disease, Type 1Cerebroside Lipidosis SyndromeGlucocerebrosidase Deficiency Disease+2 more
Genzyme, a Sanofi Company 26
Not applicableStudy completedNCT00597272
What this trial is testing

Determine Toxicity and Antibody Responses With a KLH Conjugated Bivalent Vaccine Containing GD2 Lactone, GD3 Lactone With Immunological Adjuvant QS-DG or OPT-821 in Patients With Disease Free AJCC Stage III or IV Cutaneous Melanoma

Who this might be right for
Melanoma
Memorial Sloan Kettering Cancer Center 34
Not applicableStudy completedNCT00351156
What this trial is testing

Study to Evaluate Blood Cell Lines From Patients With Gaucher Disease

Who this might be right for
Gaucher Disease
Amicus Therapeutics 50
Testing effectiveness (Phase 2)Study completedNCT00041535
What this trial is testing

OGT 918-006: A Phase I/II Randomized, Controlled Study of OGT 918 in Patients With Neuronopathic Gaucher Disease

Who this might be right for
Gaucher Disease
National Institute of Neurological Disorders and Stroke (NINDS) 30
Testing effectiveness (Phase 2)Active Not RecruitingNCT04411654
What this trial is testing

Phase 1/2 Clinical Trial of PR001 in Infants With Type 2 Gaucher Disease (PROVIDE)

Who this might be right for
Gaucher Disease, Type 2
Prevail Therapeutics 7
Post-approval studies (Phase 4)Study completedNCT04002830
What this trial is testing

A Multicenter, Safety and Efficacy Study of Taliglucerase Alfa in Subjects With Type 3 Gaucher Disease

Who this might be right for
Gaucher Disease, Type 3
Ari Zimran 14
Not applicableStudy completedNCT03519646
What this trial is testing

Eliglustat on Gaucher Disease Type IIIB

Who this might be right for
Gaucher Disease, Type III
National Taiwan University Hospital 4
Large-scale testing (Phase 3)WithdrawnNCT05815004
What this trial is testing

An Efficacy and Safety Study of AVR-RD-02 Compared to Enzyme Replacement Therapy for Treatment of Gaucher Disease Type 3

Who this might be right for
Gaucher Disease, Type 3
AVROBIO
Testing effectiveness (Phase 2)Study completedNCT01141491
What this trial is testing

Trivalent Ganglioside Vaccine With Immunological Adjuvant or Immunological Adjuvant Alone in Metastatic Sarcoma Patients Who Are Rendered Disease Free

Who this might be right for
Sarcoma
MabVax Therapeutics, Inc. 136
Not applicableEnded earlyNCT07285369
What this trial is testing

High-Dose Ambroxol in Pediatric Type III Gaucher Disease (GD3)

Who this might be right for
Gaucher Disease, Type 3
Agyany Pharma LTD 12
Not applicableLooking for participantsNCT05619900
What this trial is testing

Registry of Patients Diagnosed With Lysosomal Storage Diseases

Who this might be right for
Mucopolysaccharidosis IMucopolysaccharidosis IIMucopolysaccharidosis IV A+5 more
University of California, San Francisco 250
Not applicableEnrolling By InvitationNCT06627543
What this trial is testing

Effect of Enzyme Replacement Therapy on Cardiac Function in Children With Gaucher Disease Type 3

Who this might be right for
Gaucher Disease Type 3
Noha Osman 44
Testing effectiveness (Phase 2)Not Yet RecruitingNCT07603050
What this trial is testing

A Phase I/II Clinical Study to Evaluate the Safety and Efficacy of VGN-R08b in Patients With Type III Gaucher's Disease

Who this might be right for
Gaucher Disease Type 3
Shanghai Vitalgen BioPharma Co., Ltd. 12
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