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Results for “Non-transfusion Dependent Thalassemia”

31 trials

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Showing 20 of 31 results

Not applicableEnded earlyNCT00578292
What this trial is testing

Allogeneic Stem Cell Transplantation, Severe Homzygous 0/+Thalassemia or Sever Variants of Beta 0/+ Thalassemia, THALLO

Who this might be right for
Thalassemia
Baylor College of Medicine 10
Testing effectiveness (Phase 2)Study completedNCT04364269
What this trial is testing

Safety, Tolerability, Pharmacokinetics (PK), Pharmacodynamics (PD) and Preliminary Efficacy of VIT-2763 in β-thalassaemia

Who this might be right for
Beta-ThalassemiaNon-transfusion-dependent Thalassemia
Vifor (International) Inc. 35
Testing effectiveness (Phase 2)Study completedNCT04987489
What this trial is testing

Etavopivat in Patients With Thalassemia or Sickle Cell Disease

Who this might be right for
Sickle Cell DiseaseThalassemia
Forma Therapeutics, Inc. 53
Early research (Phase 1)WithdrawnNCT04176653
What this trial is testing

Study in Beta-thalassaemia or Myelodysplastic Syndrome Patients to Investigate the Safety and Tolerability of SLN124

Who this might be right for
Non-transfusion-dependent ThalassemiaLow Risk Myelodysplastic Syndrome
Silence Therapeutics plc
Testing effectiveness (Phase 2)Study completedNCT02993224
What this trial is testing

Open-label, Multicenter Study Assessing Preference for Deferasirox Film-coated Tablet Compared to Dispersible Tablet

Who this might be right for
Transfusion-dependent ThalassemiaNon-transfusion-dependent Thalassemia
Novartis Pharmaceuticals 148
Testing effectiveness (Phase 2)Study completedNCT00873041
What this trial is testing

Efficacy and Safety of Deferasirox in Non-transfusion Dependent Thalassemia Patients With Iron Overload and a One Year Open-label Extension Study

Who this might be right for
Non-transfusion Dependent Thalassemia
Novartis Pharmaceuticals 166
Not applicableEnded earlyNCT02179359
What this trial is testing

Hematopoietic Stem Cell Transplant for High Risk Hemoglobinopathies

Who this might be right for
Sickle Cell DiseaseTransfusion Dependent Alpha- or Beta- ThalassemiaDiamond Blackfan Anemia+5 more
Masonic Cancer Center, University of Minnesota 38
Testing effectiveness (Phase 2)Looking for participantsNCT05664737
What this trial is testing

Determine the Efficacy and Safety of Luspatercept in Adult Participants and to Evaluate the Safety and Pharmacokinetics in and Adolescent Participants With Alpha (α)-Thalassemia

Who this might be right for
Anemia
Bristol-Myers Squibb 249
Large-scale testing (Phase 3)Study completedNCT07210450
What this trial is testing

Effect of L-Glutamine on Pulmonary Artery Pressure in Patients With Non-Transfusion-Dependent Thalassemia

Who this might be right for
Pulmonary Artery PressureThalassemiaNon-transfusion Dependent Thalassemia
Mazandaran University of Medical Sciences 8
Testing effectiveness (Phase 2)Study completedNCT04054921
What this trial is testing

Safety Study for Beta Thalassemia Subjects on PTG-300

Who this might be right for
β-thalassemiaIneffective Erythropoiesis
Protagonist Therapeutics, Inc. 34
Not applicableStudy completedNCT00872339
What this trial is testing

Assessment of Pain in People With Thalassemia

Who this might be right for
Thalassemia
Carelon Research 252
Testing effectiveness (Phase 2)Study completedNCT03802201
What this trial is testing

Study of PTG-300 in Non-Transfusion Dependent and Transfusion-Dependent Beta-Thalassemia Subjects With Chronic Anemia

Who this might be right for
β-thalassemiaIneffective ErythropoiesisChronic Anemia
Protagonist Therapeutics, Inc. 63
Testing effectiveness (Phase 2)Enrolling By InvitationNCT04432623
What this trial is testing

The BENeFiTS Trial in Beta Thalassemia Intermedia

Who this might be right for
Beta Thalassemia IntermediaSickle Cell Disease
Phoenicia BioScience 36
Testing effectiveness (Phase 2)Active Not RecruitingNCT03692052
What this trial is testing

Determine the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of AG-348 in Adult Participants With Non-transfusion-dependent Thalassemia

Who this might be right for
Thalassemia
Agios Pharmaceuticals, Inc. 20
Large-scale testing (Phase 3)Study completedNCT00176852
What this trial is testing

Stem Cell Transplant for Hemoglobinopathy

Who this might be right for
Sickle Cell DiseaseThalassemiaSevere Congenital Neutropenia+2 more
Masonic Cancer Center, University of Minnesota 22
Large-scale testing (Phase 3)Active Not RecruitingNCT04770753
What this trial is testing

A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Non-Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-NTDT)

Who this might be right for
Non-Transfusion-dependent Alpha-ThalassemiaNon-Transfusion-dependent Beta-Thalassemia
Agios Pharmaceuticals, Inc. 194
Early research (Phase 1)Study completedNCT02950857
What this trial is testing

EPEG in Beta Thalassemia Patients

Who this might be right for
Beta-Thalassemia
Prolong Pharmaceuticals 6
Testing effectiveness (Phase 2)Looking for participantsNCT01962415
What this trial is testing

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

Who this might be right for
Primary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+4 more
Paul Szabolcs 100
Not applicableStudy completedNCT02626689
What this trial is testing

To Document the Burden of Illness on the Quality of Life and the Impact on Healthcare Utilization in (Beta) β-thalassemia Subjects Who Are Transfusion Dependent (TD) and Non-transfusion Dependent (NTD) Receiving Standard of Care

Who this might be right for
Beta-Thalassemia
Celgene 100
Post-approval studies (Phase 4)Study completedNCT01709838
What this trial is testing

Efficacy and Safety Study of Deferasirox in Patients With Non-transfusion Dependent Thalassemia

Who this might be right for
Non-transfusion Dependent Thalassemia
Novartis Pharmaceuticals 134
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