Testing effectiveness (Phase 2)Study completedNCT04336826
What this trial is testing
Evaluate the Safety and Pharmacokinetics of Ataluren in Participants From ≥6 Months to <2 Years of Age With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)
Who this might be right for
Nonsene Mutation Duchenne Muscular Dystrophy
PTC Therapeutics 6