Testing effectiveness (Phase 2)Not Yet RecruitingNCT05402332
What this trial is testing
Evaluating the Efficacy and Safety of D-galactose in PGM1-CDG (AVTX-801)
Who this might be right for
PGM1-CDG - Phosphoglucomutase 1-Related Congenital Disorder of Glycosylation
Eva Morava-Kozicz 8