Not applicableStudy completedNCT03999814What this trial is testingNatural History of Infantile Neuroaxonal DystrophyWho this might be right forInfantile Neuroaxonal DystrophyINAD Biojiva LLC 13
Large-scale testing (Phase 3)Active Not RecruitingNCT03570931What this trial is testingAssess Efficacy and Safety of RT001 in Subjects With Infantile Neuroaxonal DystrophyWho this might be right forInfantile Neuroaxonal Dystrophy Biojiva LLC 19
Not applicableStudy completedNCT04027816What this trial is testingA Natural History Study of Infantile Neuroaxonal DystrophyWho this might be right forNeuroaxonal Dystrophy, Infantile Biojiva LLC 43
Not applicableLooking for participantsNCT05522374What this trial is testingTIRCON International NBIA RegistryWho this might be right forNeurodegeneration With Brain Iron Accumulation (NBIA)Pantothenate Kinase-associated Neurodegeneration (PKAN)Beta-Propeller Protein-Associated Neurodegeneration (BPAN)+8 more LMU Klinikum 2,000
Post-approval studies (Phase 4)Ended earlyNCT03726996What this trial is testingDesipramine in Infantile Neuroaxonal Dystrophy (INAD).Who this might be right forInfantile Neuroaxonal Dystrophy Duke University 4
Not applicableUnknownNCT02587858What this trial is testingNBIAready: Online Collection of Natural History Patient-reported Outcome MeasuresWho this might be right forNeurodegeneration With Brain Iron Accumulation (NBIA) Susan J. Hayflick 300