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Results for “PNH”

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Showing 20 of 0 results

Not applicableActive Not RecruitingNCT05776472
What this trial is testing

A Real World Effectiveness Study of Pegcetacoplan in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Swedish Orphan Biovitrum 165
Not applicableStudy completedNCT06159816
What this trial is testing

PREVALENCE STUDY OF PNH CLONES IN PATIENTS WITH NEOPLASIES

Who this might be right for
Myeloproliferative Neoplasm
AUSL Romagna Rimini 300
Early research (Phase 1)Study completedNCT06490991
What this trial is testing

Comparison of HRS-5965 Capsules and Tablets in Healthy Subjects

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria,IgA Nephropathy
Chengdu Suncadia Medicine Co., Ltd. 16
Large-scale testing (Phase 3)Study completedNCT00122304
What this trial is testing

Study of Safety in Hemolytic Paroxysmal Nocturnal Hemoglobinuria (PNH) Patients Treated With Eculizumab

Who this might be right for
Hemoglobinuria, Paroxysmal
Alexion Pharmaceuticals, Inc. 85
Early research (Phase 1)Study completedNCT03316521
What this trial is testing

First-In-Human Clinical Study of the C3 Complement Inhibitor AMY- 101 in Healthy Male Volunteers

Who this might be right for
Complement Mediated Diseases
Amyndas Pharmaceuticals S.A. 50
Large-scale testing (Phase 3)Study completedNCT00130000
What this trial is testing

Eculizumab to Treat Paroxysmal Nocturnal Hemoglobinuria

Who this might be right for
Paroxysmal Hemoglobinuria, Nocturnal
National Heart, Lung, and Blood Institute (NHLBI) 87
Testing effectiveness (Phase 2)Study completedNCT00143559
What this trial is testing

Stem Cell Transplantation as Immunotherapy for Hematologic Malignancies

Who this might be right for
LeukemiaAcute Lymphoblastic LeukemiaAcute Myeloid Leukemia+6 more
St. Jude Children's Research Hospital 17
Early research (Phase 1)Study completedNCT05490017
What this trial is testing

To Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Escalating Single and Multiple Doses of KP104

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Kira Pharmacenticals (US), LLC. 80
Testing effectiveness (Phase 2)Study completedNCT00975975
What this trial is testing

Basiliximab #2: In-Vivo Activated T-Cell Depletion to Prevent Graft-Versus_Host Disease (GVHD) After Nonmyeloablative Allotransplantation for the Treatment of Blood Cancer

Who this might be right for
Acute Myelogenous LeukemiaAcute Lymphocytic LeukemiaChronic Myelogenous Leukemia+8 more
Indiana University 17
Large-scale testing (Phase 3)Looking for participantsNCT06934967
What this trial is testing

Study to Assess the Pharmacokinetics, Safety, and Tolerability of Iptacopan in Pediatric PNH Patients

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Novartis Pharmaceuticals 12
Not applicableEnrolling By InvitationNCT07657052
What this trial is testing

A Multicenter, Open-label Study Evaluating the Long-term Safety and Efficacy of XH-S003 Capsules in Patients With Paroxysmal Nocturnal Hemoglobinuria

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
S-INFINITY Pharmaceuticals Co., Ltd 26
Testing effectiveness (Phase 2)Study completedNCT03946748
What this trial is testing

Study to Evaluate the Efficacy and Safety of REGN3918 in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Regeneron Pharmaceuticals 24
Large-scale testing (Phase 3)Not Yet RecruitingNCT07177872
What this trial is testing

A Long-term Efficacy and Safety of NTQ5082 Capsules

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Nanjing Chia-tai Tianqing Pharmaceutical 78
Early research (Phase 1)Study completedNCT05889299
What this trial is testing

Study of the Safety and Efficacy of OMS906 in Patients With Paroxysmal Nocturnal Hemoglobinuria

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Omeros Corporation 15
Large-scale testing (Phase 3)Study completedNCT00112983
What this trial is testing

Eculizumab in Treating Patients With Paroxysmal Nocturnal Hemoglobinuria

Who this might be right for
Leukemia
Jonsson Comprehensive Cancer Center
Early research (Phase 1)UnknownNCT06543459
What this trial is testing

To Evaluate the Effect of Single Oral Dose of MY008211A Tablets on QTc Interval in Healthy Subjects

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Wuhan Createrna Science and Technology Co., Ltd 16
Not applicableNot Yet RecruitingNCT07108023
What this trial is testing

Hematological Disorders in EHPVO Patients

Who this might be right for
Extrahepatic Portal Vein Obstruction (EHPVO)ThrombophiliaMyeloproliferative Neoplasms (MPN)+5 more
Rahab Nady 115
Large-scale testing (Phase 3)Not Yet RecruitingNCT07177859
What this trial is testing

A Phase III Study of NTQ5082 Capsules in the Treatment of Paroxysmal Nocturnal Hemoglobinuria Patients

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Nanjing Chia-tai Tianqing Pharmaceutical 78
Not applicableEnrolling By InvitationNCT07102849
What this trial is testing

Molecular and Clinical Analysis of Bone Marrow Failure: A Secondary Research Study

Who this might be right for
Bone Marrow Failure DisordersVEXAS SyndromeHemoglobinurea, Paroxysmal+2 more
National Heart, Lung, and Blood Institute (NHLBI) 1,400
Large-scale testing (Phase 3)Study completedNCT02946463
What this trial is testing

ALXN1210 (Ravulizumab) Versus Eculizumab in Complement Inhibitor Treatment-Naïve Adult Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH)

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Alexion Pharmaceuticals, Inc. 272
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