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Results for “Peroxisome Biogenesis Disorders”

3 trials

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Showing 3 of 3 results

Large-scale testing (Phase 3)Study completedNCT01838941
What this trial is testing

Betaine and Peroxisome Biogenesis Disorders

Who this might be right for
Peroxisome Biogenesis Disorders
McGill University Health Centre/Research Institute of the McGill University Health Centre 12
Testing effectiveness (Phase 2)Study completedNCT03856866
What this trial is testing

Hydroxychloroquine Administration for Reduction of Pexophagy

Who this might be right for
Zellweger SyndromePeroxisome Biogenesis Disorders
The Hospital for Sick Children 3
Not applicableLooking for participantsNCT01668186
What this trial is testing

Longitudinal Natural History Study of Patients With Peroxisome Biogenesis Disorders (PBD)

Who this might be right for
Peroxisome Biogenesis DisorderZellweger Spectrum DisorderRCDP - Rhizomelic Chondrodysplasia Punctata+8 more
McGill University Health Centre/Research Institute of the McGill University Health Centre 244