Not applicableStudy completedNCT05431127What this trial is testingHigh Dose Inspiratory Muscle Training in LOPDWho this might be right forLate-Onset Pompe DiseaseLysosomal Disease Duke University 34
Large-scale testing (Phase 3)Study completedNCT03729362What this trial is testingA Study Comparing ATB200/AT2221 With Alglucosidase Alfa/Placebo in Adult Subjects With Late-onset Pompe DiseaseWho this might be right forPompe Disease (Late-onset) Amicus Therapeutics 125
Not applicableEnded earlyNCT02221362What this trial is testingA Prospective, Noninterventional, Observational Study of Late-Onset Pompe DiseaseWho this might be right forLate-onset Pompe Patients Untreated or Treated With rhGAA BioMarin Pharmaceutical 30
Not applicableLooking for participantsNCT00231400What this trial is testingPompe Disease Registry ProtocolWho this might be right forGlycogen Storage Disease Type IIPompe Disease Genzyme, a Sanofi Company 2,000
Very early researchStudy completedNCT06109948What this trial is testingStudy to Assess the Safety, Tolerability, PK and PD of ABX1100Who this might be right forHealthyLate Onset Pompe Disease Aro Biotherapeutics 46
Testing effectiveness (Phase 2)Looking for participantsNCT07123155What this trial is testingStudy of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)Who this might be right forPompe Disease Shionogi 45
Large-scale testing (Phase 3)Active Not RecruitingNCT03911505What this trial is testingZIP Study-OL Study of Safety, PK, Efficacy, PD, Immunogenicity of ATB200/AT2221 in Pediatrics Aged 0 to < 18 y.o. w/LOPDWho this might be right forPompe Disease (Late-onset) Amicus Therapeutics 21
Not applicableEnded earlyNCT02191917What this trial is testingRespiratory Muscle Strength in Patients With Late-onset Pompe Disease (LOPD)Who this might be right forLate-onset Pompe Disease BioMarin Pharmaceutical 8
Not applicableStudy completedNCT04907162What this trial is testingMusculoskeletal Nociceptive Pain in Participants With Neuromuscular DisordersWho this might be right forPompe Disease (Late-onset)Myotonic Dystrophy Type 1 (DM1)Myotonic Dystrophy Type 2+4 more LMU Klinikum 82
Early research (Phase 1)Study completedNCT03533673What this trial is testingAAV2/8-LSPhGAA (ACTUS-101) in Late-Onset Pompe DiseaseWho this might be right forPompe Disease AskBio Inc 7
Large-scale testing (Phase 3)Study completedNCT00268944What this trial is testingSafety and Effectiveness Study of rhGAA in Patients With Advanced Late-Onset Pompe Disease Receiving Respiratory SupportWho this might be right forPompe Disease (Late-onset)Glycogen Storage Disease Type II (GSD-II)Acid Maltase Deficiency Disease+1 more Genzyme, a Sanofi Company 5
Early research (Phase 1)Looking for participantsNCT07354724What this trial is testingEvaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe DiseaseWho this might be right forLate-onset Pompe Disease Denali Therapeutics Inc. 32
Not applicableStudy completedNCT03893240What this trial is testingNeutralizing Antibody Seroprevalence Study With a Retrospective Component in Participants With Late-Onset Pompe DiseaseWho this might be right forPompe DiseasePompe Disease (Late-onset)Glycogen Storage Disease Type 2+3 more Spark Therapeutics, Inc. 61
Post-approval studies (Phase 4)Study completedNCT04676373What this trial is testingStudy to Evaluate Efficacy and Safety in Chinese Patients With Late Onset Pompe Disease With Alglucosidase Alfa TreatmenWho this might be right forPompe's Disease Genzyme, a Sanofi Company 41
Not applicableUnknownNCT00713245What this trial is testingA Long Term Follow up Study in Late-onset Pompe DiseaseWho this might be right forPompe Disease National Taiwan University Hospital 70
Not applicableLooking for participantsNCT07478172What this trial is testingEffects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular DiseaseWho this might be right forNeuromuscular Diseases (NMD)Amyotrophic Lateral SclerosisMyasthenia Gravis+15 more University of Missouri-Columbia 50
Testing effectiveness (Phase 2)UnknownNCT06130228What this trial is testingNutritional Therapy in Late-onset Pompe DiseaseWho this might be right forPompe DiseaseMuscle LossObesity+5 more McMaster University 28
Large-scale testing (Phase 3)Study completedNCT04138277What this trial is testingAssess the Long-term Safety and Efficacy of ATB200/AT2221 in Adult Subjects With Late-Onset Pompe Disease (LOPD)Who this might be right forPompe Disease (Late-onset) Amicus Therapeutics 119
Early research (Phase 1)Study completedNCT01859624What this trial is testingAlbuterol in Individuals With Late Onset Pompe Disease (LOPD)Who this might be right forPompe Disease Duke University 8
Not applicableUnknownNCT05951790What this trial is testingInspiratory Muscle Training (IMT) in Adult People With Pompe DiseaseWho this might be right forGlycogen Storage Disease Type IIPompe Disease (Late-onset) Fondazione Don Carlo Gnocchi Onlus 20