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Results for “Pompe Disease Late-Onset”

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Showing 20 of 0 results

Testing effectiveness (Phase 2)Looking for participantsNCT07123155
What this trial is testing

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

Who this might be right for
Pompe Disease
Shionogi 45
Early research (Phase 1)Study completedNCT03533673
What this trial is testing

AAV2/8-LSPhGAA (ACTUS-101) in Late-Onset Pompe Disease

Who this might be right for
Pompe Disease
AskBio Inc 7
Testing effectiveness (Phase 2)Study completedNCT01885936
What this trial is testing

Safety and Efficacy of Albuterol in Individuals With Late-onset Pompe Disease

Who this might be right for
Pompe Disease
Duke University 16
Not applicableStudy completedNCT04907162
What this trial is testing

Musculoskeletal Nociceptive Pain in Participants With Neuromuscular Disorders

Who this might be right for
Pompe Disease (Late-onset)Myotonic Dystrophy Type 1 (DM1)Myotonic Dystrophy Type 2+4 more
LMU Klinikum 82
Early research (Phase 1)Study completedNCT02240407
What this trial is testing

Re-administration of Intramuscular AAV9 in Patients With Late-Onset Pompe Disease

Who this might be right for
Pompe Disease
University of Florida 2
Post-approval studies (Phase 4)Study completedNCT01288027
What this trial is testing

Exploratory Muscle Biopsy Assessment Study in Patients With Late-Onset Pompe Disease Treated With Alglucosidase Alfa

Who this might be right for
Pompe Disease (Late-Onset)Glycogen Storage Disease Type II (GSD II)Glycogenesis 2 Acid Maltase Deficiency
Genzyme, a Sanofi Company 16
Not applicableStudy completedNCT00731081
What this trial is testing

Study About the Evolution of Severe Late Onset Pompe Disease Patient With Pulmonary Dysfunction and Receiving Myozyme®

Who this might be right for
Pompe Disease (Late-Onset)Glycogen Storage Disease Type II (GSD II)Glycogenesis 2 Acid Maltase Deficiency
Genzyme, a Sanofi Company 8
Large-scale testing (Phase 3)Study completedNCT03729362
What this trial is testing

A Study Comparing ATB200/AT2221 With Alglucosidase Alfa/Placebo in Adult Subjects With Late-onset Pompe Disease

Who this might be right for
Pompe Disease (Late-onset)
Amicus Therapeutics 125
Not applicableStudy completedNCT02824068
What this trial is testing

Long-term Outcome in Late-onset Pompe Disease Treated Beyond 36 Months (STIG-Pompe-Study)

Who this might be right for
Pompe Disease
LMU Klinikum 112
Not applicableStudy completedNCT05431127
What this trial is testing

High Dose Inspiratory Muscle Training in LOPD

Who this might be right for
Late-Onset Pompe DiseaseLysosomal Disease
Duke University 34
Large-scale testing (Phase 3)Study completedNCT00125879
What this trial is testing

Extension Study of Patients With Infantile-Onset Pompe Disease Who Were Previously Enrolled in Protocol AGLU01602

Who this might be right for
Glycogen Storage Disease Type II
Genzyme, a Sanofi Company 16
Testing effectiveness (Phase 2)Active Not RecruitingNCT04093349
What this trial is testing

A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE)

Who this might be right for
Pompe DiseasePompe Disease (Late-onset)Glycogen Storage Disease Type 2+4 more
Spark Therapeutics, Inc. 4
Not applicableActive Not RecruitingNCT03694561
What this trial is testing

Developing a Management Approach for Patients With "Late-Onset" Pompe Disease

Who this might be right for
Pompe DiseasePompe Disease (Late-onset)GAA Deficiency
Duke University 20
Not applicableStudy completedNCT04120168
What this trial is testing

Study Determining the Frequency of Duchenne Muscular Dystrophy and Late-onset Pompe Disease

Who this might be right for
Duchenne Muscular DystrophyPompe Disease (Late-onset)
Turkish Society of Pediatric Gastroenterology, Hepatology and Nutrition 590
Not applicableStudy completedNCT03255213
What this trial is testing

Lingual Muscle Training in Late-Onset Pompe Disease (LOPD)

Who this might be right for
Glycogen Storage Disease
Duke University 5
Testing effectiveness (Phase 2)Study completedNCT00765414
What this trial is testing

Extension Study of Long-term Safety and Efficacy of Myozyme for a Single Patient With Pompe Disease Who Were Previously Enrolled in Genzyme Sponsored ERT Studies.

Who this might be right for
Pompe Disease Late-OnsetGlycogen Storage Disease Type II GSD II
Genzyme, a Sanofi Company 1
Not applicableStudy completedNCT03285126
What this trial is testing

Pompe Gene Therapy- Screening for Eligibility

Who this might be right for
Pompe Disease (Late-onset)
Duke University 19
Post-approval studies (Phase 4)Study completedNCT00455195
What this trial is testing

Late-Onset Treatment Study Extension Protocol

Who this might be right for
Pompe Disease (Late-Onset)Glycogen Storage Disease Type II (GSD-II)Glycogenesis Type II+1 more
Genzyme, a Sanofi Company 81
Not applicableStudy completedNCT02354664
What this trial is testing

Dynamic Respiratory Muscle Function in Late-Onset Pompe Disease

Who this might be right for
Pompe Disease
University of Florida 14
Not applicableLooking for participantsNCT07478172
What this trial is testing

Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease

Who this might be right for
Neuromuscular Diseases (NMD)Amyotrophic Lateral SclerosisMyasthenia Gravis+15 more
University of Missouri-Columbia 50
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