Not applicableUnknownNCT05257005
What this trial is testing
Natural History Study of Pyruvate Dehydrogenase Deficiency
Who this might be right for
Pyruvate Dehydrogenase Complex DeficiencyPyruvate Dehydrogenase E1 Alpha DeficiencyPyruvate Dehydrogenase E1-Beta Deficiency+2 more
Great Ormond Street Hospital for Children NHS Foundation Trust 50