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Results for “RARE DISEASE”

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Showing 20 of 0 results

Testing effectiveness (Phase 2)Study completedNCT00004493
What this trial is testing

Phase II Pilot Randomized Study of Sodium Dichloroacetate in Patients With Congenital Lactic Acidemia

Who this might be right for
Lactic Acidosis
University of California, San Diego 75
Testing effectiveness (Phase 2)Study completedNCT00004763
What this trial is testing

Phase II Randomized Study of Leuprolide Vs Oral Contraceptive Therapy Vs Leuprolide and Oral Contraceptive Therapy for Ovarian Hyperandrogenism

Who this might be right for
Hyperandrogenism
National Center for Research Resources (NCRR) 45
Testing effectiveness (Phase 2)Study completedNCT01761292
What this trial is testing

Assess Safety/Tolerability, pk, Effects on Histology, Clinical Parameters of Givinostat in Children With DMD

Who this might be right for
Duchenne Muscular Dystrophy (DMD)
Italfarmaco 20
Not applicableUnknownNCT00006129
What this trial is testing

Randomized Study of Testosterone and Progressive Resistance Exercise in Men With Burn Injury

Who this might be right for
Burns
National Center for Research Resources (NCRR) 60
Testing effectiveness (Phase 2)Study completedNCT00004665
What this trial is testing

Phase II Study of Long-Term Dehydroepiandrosterone for Systemic Lupus Erythematosus

Who this might be right for
Systemic Lupus Erythematosus
National Center for Research Resources (NCRR) 20
Not applicableLooking for participantsNCT02461615
What this trial is testing

A National Registry For Pulmonary Alveolar Proteinosis

Who this might be right for
Pulmonary Alveolar Proteinosis
Children's Hospital Medical Center, Cincinnati 500
Large-scale testing (Phase 3)Ended earlyNCT00004465
What this trial is testing

Phase III Randomized Study of SYNSORB Pk in Children With E. Coli-Associated Hemolytic Uremic Syndrome

Who this might be right for
Hemolytic Uremic Syndrome
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) 145
Not applicableStudy completedNCT06935578
What this trial is testing

RAre, But Not aLone: a Large Italian Network to Empower the Impervious diaGNostic Pathway of Rare cerEbrovascular Diseases (ALIGNED)

Who this might be right for
CADASILCADASIL (Diagnosis)Moya Moya Disease+5 more
Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta 500
Testing effectiveness (Phase 2)Study completedNCT05358717
What this trial is testing

Evaluate the Safety and Efficacy of PTC518 in Participants With Huntington's Disease (HD)

Who this might be right for
Huntington Disease
Novartis Pharmaceuticals 159
Testing effectiveness (Phase 2)Looking for participantsNCT05800340
What this trial is testing

Neoadjuvant Immunotherapy in Rare Mutations Localized NSCLC

Who this might be right for
Non-Small Cell Lung CancerRET Driver MutationBRAF V600 Mutation+3 more
Guangdong Provincial People's Hospital 30
Not applicableLooking for participantsNCT05903261
What this trial is testing

Prospective Observational Basket Study of Stereotactic Body Radiation Therapy for OligoMetastatic Patients From Rare Tumors

Who this might be right for
Oligometastatic Disease
Istituto Clinico Humanitas 200
Not applicableLooking for participantsNCT02543996
What this trial is testing

Human Biospecimen Procurement Protocol: Biorepository to Support Translational Research to Identify Disease Mechanism(s)

Who this might be right for
Undiagnosed DiseasesCardiovascular Disease
National Heart, Lung, and Blood Institute (NHLBI) 10,000
Early research (Phase 1)Looking for participantsNCT07776626
What this trial is testing

Phase I Exploratory Study of YOLT-203 in Patients With Primary Hyperoxaluria Type 1 (PH1)

Who this might be right for
Primary Hyperoxaluria Type 1PH1
YolTech Therapeutics Co., Ltd 9
Not applicableStudy completedNCT00004478
What this trial is testing

Droxidopa in Treating Patients With Neurogenic Hypotension

Who this might be right for
Shy-Drager SyndromeOrthostatic Hypotension
Icahn School of Medicine at Mount Sinai
Large-scale testing (Phase 3)Study completedNCT00004376
What this trial is testing

Phase III Randomized, Double-Blind, Placebo-Controlled Study of Guanfacine for Tourette Syndrome and Attention Deficit Hyperactivity Disorder

Who this might be right for
Tourette Syndrome
National Center for Research Resources (NCRR) 35
Testing effectiveness (Phase 2)Study completedNCT05998395
What this trial is testing

JAK/STAT Inhibition in CNS Kohlmeier-Degos Disease

Who this might be right for
Kohlmeier Degos Disease With Neurologic InvolvementKohlmeier-Degos Disease
National Heart, Lung, and Blood Institute (NHLBI) 1
Not applicableLooking for participantsNCT04398628
What this trial is testing

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

Who this might be right for
Hematologic DisorderBleeding DisorderConnective Tissue Disorder+10 more
American Thrombosis and Hemostasis Network 3,000
Large-scale testing (Phase 3)Study completedNCT06596135
What this trial is testing

Open-Label Extension Study of Setmelanotide

Who this might be right for
Obesity Associated With Defects in Leptin-melanocortin Pathway
Rhythm Pharmaceuticals, Inc. 28
Not applicableLooking for participantsNCT04777175
What this trial is testing

A Retrospective Study: Evaluation of the Efficacy of Immunotherapy With Rare Mutations in Non-small Cell Lung Cancer

Who this might be right for
Non Small Cell Lung Cancer
Yongchang Zhang 186
Large-scale testing (Phase 3)Study completedNCT00004421
What this trial is testing

Deep Brain Stimulation in Treating Patients With Dystonia

Who this might be right for
Dystonia
Icahn School of Medicine at Mount Sinai 15
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