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Results for “RARE DISEASE”

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Showing 20 of 0 results

Not applicableLooking for participantsNCT07205861
What this trial is testing

Retrospective Epidemiological Study of Patients in the National Cohort of the French TMA Center

Who this might be right for
Thrombotic Thrombocytopenic Purpura (TTP)Immune Thrombotic Thrombocytopenic PurpuraThrombotic Microangiopathies+5 more
Assistance Publique - Hôpitaux de Paris 1,200
Testing effectiveness (Phase 2)Looking for participantsNCT07070232
What this trial is testing

A Clinical Study to Test if an Investigational Treatment Called BNT326 is Safe and Potentially Beneficial When Used Alone or in Combination With Other Investigational Treatments Such as BNT327, for People With Advanced Malignant Tumors

Who this might be right for
Advanced Solid Tumor
BioNTech SE 1,438
Not applicableStudy completedNCT00004444
What this trial is testing

Pilot Randomized Study of Paromomycin (Aminosidine) vs Streptomycin for Uncomplicated Pulmonary Tuberculosis

Who this might be right for
Tuberculosis, Pulmonary
FDA Office of Orphan Products Development 24
Testing effectiveness (Phase 2)Looking for participantsNCT06525636
What this trial is testing

A First-in-human Study of KK8123 in Adults With X-linked Hypophosphatemia

Who this might be right for
X-linked Hypophosphatemia
Kyowa Kirin Co., Ltd. 39
Early research (Phase 1)Study completedNCT00004828
What this trial is testing

Liothyronine in Children With Single Ventricle Congenital Cardiac Malformations Undergoing the Fontan Procedure

Who this might be right for
Tricuspid AtresiaHeart Defects, Congenital
FDA Office of Orphan Products Development 28
Large-scale testing (Phase 3)Study completedNCT00004772
What this trial is testing

Phase III Randomized, Double-Blind, Placebo-Controlled Study of Intravenous Immune Globulin for Chronic Inflammatory Demyelinating Polyneuropathy

Who this might be right for
Polyradiculoneuropathy, Chronic Inflammatory Demyelinating
National Center for Research Resources (NCRR) 90
Early research (Phase 1)UnknownNCT00005896
What this trial is testing

Phase I Pilot Study of CD34 Enriched, Fanconi's Anemia Complementation Group C Gene Transduced Autologous Peripheral Blood Stem Cell Transplantation in Patients With Fanconi's Anemia

Who this might be right for
Fanconi's Anemia
University of Minnesota 6
Testing effectiveness (Phase 2)Active Not RecruitingNCT07105384
What this trial is testing

Quantification Tools for a Novel Tau PET Marker in a Rare Neurological Disease: 18F-PI-2620 in Progressive Supranuclear Palsy

Who this might be right for
Parkinson Disease
Fundacion Clinic per a la Recerca Biomédica 66
Not applicableStudy completedNCT06397443
What this trial is testing

Ready to Sail: Evaluating Sailing's Feasibility as Ergotherapy

Who this might be right for
Multiple OsteochondromaOllier DiseaseOsteogenesis Imperfecta
Istituto Ortopedico Rizzoli 8
Testing effectiveness (Phase 2)Active Not RecruitingNCT04482309
What this trial is testing

T-DXd in Patients With Selected HER2 Expressing Tumors

Who this might be right for
Part 1: Bladder, Biliary Tract, Cervical, Endometrial, Ovarian, Pancreatic Cancer, Rare Tumors, Any Tumor Type Excluding Breast, Gastric, Colorectal CancerPart 2: HER2 Expressing/Amplified Solid Tumors Excluding Breast, Gastric, Colorectal Cancer
AstraZeneca 477
Not applicableStudy completedNCT04795206
What this trial is testing

Natural Disease Progression in Participants With Choroideremia

Who this might be right for
Choroideremia
Biogen 1,178
Not applicableStudy completedNCT00004441
What this trial is testing

Study of Tauroursodeoxycholic Acid for Hepatobiliary Disease in Cystic Fibrosis

Who this might be right for
Cystic Fibrosis
Children's Hospital Medical Center, Cincinnati 39
Not applicableStudy completedNCT02706639
What this trial is testing

Williams Syndrome (WS) and Supravalvar Aortic Stenosis (SVAS) DNA and Tissue Bank

Who this might be right for
Williams SyndromeSupravalvular Aortic StenosisCardiovascular Disease
National Heart, Lung, and Blood Institute (NHLBI) 305
Not applicableStudy completedNCT07428941
What this trial is testing

Evaluating an Artificial Intelligence Tool to Help Primary Care Doctors Diagnose Skin Conditions.

Who this might be right for
Skin LesionsMelanocytic NeviMelanoma (Skin Cancer)+6 more
AI Labs Group S.L 9
Not applicableStudy completedNCT00014781
What this trial is testing

Study of Hepatic Glucose Production and De Novo Lipogenesis in Patients With Cystic Fibrosis

Who this might be right for
Cystic Fibrosis
University of Utah 39
Not applicableNot Yet RecruitingNCT07680751
What this trial is testing

European Cystinosis Cohort 2

Who this might be right for
Cystinosis
Institut National de la Santé Et de la Recherche Médicale, France 250
Not applicableStudy completedNCT00004423
What this trial is testing

Controlled Trial of 4-Aminosalicylic Acid in Patients With Small Bowel Crohn's Disease

Who this might be right for
Crohn's Disease
University of Vermont 80
Not applicableNot Yet RecruitingNCT07662694
What this trial is testing

CLASSIFY-OMM: Multicenter Rare Disease Cohort for T-Stage Reclassification and Molecular Subtyping-Based Precision Therapy in Oral Mucosal Melanoma

Who this might be right for
Mucosal Melanoma of the Head and NeckOral Melanoma
Shanghai Ninth People's Hospital Affiliated to Shanghai Jiao Tong University 1,100
Testing effectiveness (Phase 2)Study completedNCT01573754
What this trial is testing

Hydroxychloroquine and Phlebotomy for Treating Porphyria Cutanea Tarda

Who this might be right for
Porphyria Cutanea Tarda
The University of Texas Medical Branch, Galveston 48
Large-scale testing (Phase 3)Study completedNCT00004795
What this trial is testing

Phase II/III Randomized, Double-Blind, Placebo-Controlled Study of Dehydroepiandrosterone in Women With Mild to Moderate Systemic Lupus Erythematosus

Who this might be right for
Systemic Lupus Erythematosus
National Center for Research Resources (NCRR) 190
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